bims-drudre Biomed News
on Targeted drug delivery and programmed release mechanisms
Issue of 2023–01–08
ten papers selected by
Ceren Kimna, Technical University of Munich



  1. bioRxiv. 2022 Dec 22. pii: 2022.12.22.521490. [Epub ahead of print]
      Ionizable lipid nanoparticles (LNPs) have gained attention as mRNA delivery platforms for vaccination against COVID-19 and for protein replacement therapies. LNPs enhance mRNA stability, circulation time, cellular uptake, and preferential delivery to specific tissues compared to mRNA with no carrier platform. However, LNPs have yet to be developed for safe and effective mRNA delivery to the placenta as a method to treat placental dysfunction. Here, we develop LNPs that enable high levels of mRNA delivery to trophoblasts in vitro and to the placenta in vivo with no toxicity. We conducted a Design of Experiments to explore how LNP composition, including the type and molar ratio of each lipid component, drives trophoblast and placental delivery. Our data revealed that a specific combination of ionizable lipid and phospholipid in the LNP design yields high transfection efficiency in vitro . Further, we present one LNP platform that exhibits highest delivery of placental growth factor mRNA to the placenta in pregnant mice, which demonstrates induced protein synthesis and secretion of a therapeutic protein. Lastly, our high-performing LNPs have no toxicity to both the pregnant mice and fetuses. Our results demonstrate the feasibility of LNPs as a platform for mRNA delivery to the placenta. Our top LNPs may provide a therapeutic platform to treat diseases that originate from placental dysfunction during pregnancy.
    DOI:  https://doi.org/10.1101/2022.12.22.521490
  2. ACS Nano. 2023 Jan 03.
      Oral administration of protein drugs has always been challenging owing to various intestinal barriers. Herein, we developed an efficient oral protein delivery strategy by using in situ polymerization of zwitterions to encapsulate proteins, which were then loaded into enteric coated capsules for oral feeding. After oral administration of such capsules, the enteric coating would be degraded once the capsule enters the intestine, releasing polyzwitterion/protein nanocomplexes. With the help of polyzwitterion modification, such nanocomplexes were able to pass through the mucus and cellular barriers, likely by the proton-assisted amino acid transporter 1 (PAT1) pathway. Such a polyzwitterion-based protein encapsulation strategy could allow for effective oral delivery of different proteins, including bovine serum albumin (BSA), insulin, and antibodies. Using this strategy, the oral bioavailabilities of insulin and immunoglobin G (IgG) were measured to be as high as 16.9% and 12.5%, respectively. Notably, oral feeding of polyzwitterion/insulin capsules could effectively lower the blood glucose level of diabetic animals (mice, rats, and pigs). Moreover, polyzwitterion/antiprogramed death-1 (αPD-1) capsules were able to induce efficient antitumor immune responses, showing significant tumor inhibition effects toward B16F10- and 4T1-tumor bearing mouse models after oral administration. No significant toxic effect was observed for such oral protein formulations in the treated animals. Our work presents a strategy for the efficient oral delivery of protein drugs, including those with large molecular weights (e.g., antibodies) that can hardly be orally delivered using existing technologies.
    Keywords:  capsules; oral delivery; polyzwitterion; protein drugs; proton assisted amino acid transporter 1 pathway
    DOI:  https://doi.org/10.1021/acsnano.2c08434
  3. ACS Nano. 2023 Jan 05.
      Chemoresistance is a formidable issue in clinical anticancer therapy and is pertinent to the lowered efficacies of chemotherapeutics and the activated tumor self-repairing proceedings. Herein, bifunctional amphiphiles containing galactose ligands and high-density disulfide are synthesized for encapsulating mitochondrion-targeting tetravalent platinum prodrugs to construct a cascade targeted and mitochondrion-dysfunctional nanomedicine (Gal-NP@TPt). Subsequent investigations verify that Gal-NP@TPt with sequential targeting functions toward tumors and mitochondria improved the spatiotemporal level of platinum. In addition, glutathione depletion by Gal-NP@TPt appear to substantially inhibit the proceedings of platinum detoxification, inducing the susceptibility to the mitochondrial platinum. Moreover, the strategic transportation of platinum to mitochondria lacking DNA repair machinery by Gal-NP@TPt lowers the possibility of platinum deactivation. Eventually, Gal-NP@TPt demonstrates appreciable antitumor effects for the systemic treatment of patient-derived tumor xenografts of hepatocellular carcinoma. Note that these strategies in overcoming drug resistance have also been confirmed to be valid based on genome-wide analysis via RNA-sequencing. Therefore, an intriguing multifunctional nanomedicine capable of resolving formidable chemoresistance is achieved, which should be greatly emphasized in practical applications for the treatment of intractable tumors.
    Keywords:  RNA-sequencing; cascade targeting; drug resistance; glutathione depletion; mitochondrial dysfunction
    DOI:  https://doi.org/10.1021/acsnano.2c09342
  4. Adv Healthc Mater. 2023 Jan 05. e2203026
      Currently, tumor immunotherapy is becoming a new revolution in tumor treatment. Generated from tumor cell lysate or irradiated tumor cells, the whole tumor antigen-based vaccines have the possibility to enhance antitumor immune response without survival from immune surveillance in personalized immunotherapy. Here, polydopamine nanoparticles (PDA NPs) after self-polymerization were covalently coated with tumor cell lysate (TCL) to form PDA@CL. Engineered salmonella (EnS) wrapped with PDA@CL (EnS@PDA@CL) was targeted the localization in the tumor site by intravenous administration. EnS@PDA@CL delivered autologous antigen-containing nanoparticles to tumor hypoxia regions through blood circulation. The PDA@CL particles promoted the maturation of dendritic cells, thus eliciting the infiltration of whole tumor antigens specific cytotoxic T lymphocytes, significantly triggering antitumor immunity. The tumor regression in the Panc02 mice confirmed the therapeutic potential of EnS@PDA@CL in clinical personalized immunotherapy. This article is protected by copyright. All rights reserved.
    Keywords:  Engineered salmonella; personalized immunotherapy; polydopamine nanoparticles; whole tumor antigens
    DOI:  https://doi.org/10.1002/adhm.202203026
  5. J Control Release. 2023 Jan 02. pii: S0168-3659(23)00001-9. [Epub ahead of print]
      Bladder cancer (BCa) is one of the most prevalent cancers worldwide. The effectiveness of intravesical therapy for bladder cancer, however, is limited due to the short dwell time and the presence of permeation barriers. Considering the histopathological features of BCa, the permeation barriers for drugs to transport across consist of a mucus layer and a nether tumor physiological barrier. Mucoadhesive delivery systems or mucus-penetrating delivery systems are developed to enhance their retention in or penetration across the mucus layer, but delivery systems that are capable of mucoadhesion-to-mucopenetration transition are more efficient to deliver drugs across the mucus layer. For the tumor physiological barrier, delivery systems mainly rely on four types of penetration mechanisms to cross it. This review summarizes the classical and latest approaches to intravesical drug delivery systems to penetrate BCa.
    Keywords:  Bladder cancer; Drug delivery; Intravesical therapy; Penetration; Transport
    DOI:  https://doi.org/10.1016/j.jconrel.2023.01.001
  6. ACS Nano. 2023 Jan 05.
      Nanoparticles (NPs) and other engineered nanomaterials have great potential as nanodrugs or nanomedical devices for biomedical applications. However, the adsorption of proteins in blood circulation or similar physiological fluids can significantly alter the surface properties and therapeutic response induced by most nanomaterials. For example, interaction with proteins can change the bloodstream circulation time and availability of therapeutic NPs or hinder the accumulation in their desired target organs. Proteins can also trigger or prevent agglomeration. By combining experimental and computational approaches, we have developed NPs carrying polyethylene glycol (PEG) polymeric coatings that mimic the surface charge distribution of proteins typically found in blood, which are known to show low aggregation under normal blood conditions. Here, we show that NPs with coatings based on apoferritin or human serum albumin display better antifouling properties and weaker protein interaction compared to similar NPs carrying conventional PEG polymeric coatings.
    Keywords:  antifouling; biomimetic surface coating; colloidal nanoparticles; molecular dynamics; polyethylene glycol; protein adsorption
    DOI:  https://doi.org/10.1021/acsnano.2c05682
  7. Proc Natl Acad Sci U S A. 2023 Jan 10. 120(2): e2211977120
      Engineered microbes for the delivery of biologics are a promising avenue for the treatment of various conditions such as chronic inflammatory disorders and metabolic disease. In this study, we developed a genetically engineered probiotic delivery system that delivers a peptide to the intestinal tract with high efficacy. We constructed an inducible system in the probiotic Lactobacillus reuteri to secrete the Kv1.3 potassium blocker ShK-235 (LrS235). We show that LrS235 culture supernatants block Kv1.3 currents and preferentially inhibit human T effector memory (TEM) lymphocyte proliferation in vitro. A single oral gavage of healthy rats with LrS235 resulted in sufficient functional ShK-235 in the circulation to reduce inflammation in a delayed-type hypersensitivity model of atopic dermatitis mediated by TEM cells. Furthermore, the daily oral gavage of LrS235 dramatically reduced clinical signs of disease and joint inflammation in rats with a model of rheumatoid arthritis without eliciting immunogenicity against ShK-235. This work demonstrates the efficacy of using the probiotic L. reuteri as a novel oral delivery platform for the peptide ShK-235 and provides an efficacious strategy to deliver other biologics with great translational potential.
    Keywords:  Kv1.3 channel; drug delivery; synthetic biology
    DOI:  https://doi.org/10.1073/pnas.2211977120
  8. Adv Mater. 2023 Jan 05. e2207101
      Additive manufacturing at the micro- and nanoscale has seen a recent upsurge to suit an increasing demand for more elaborate structures. However, the integration and precise placement of multiple distinct materials at small scales remain a challenge. To this end, we combine here capillarity-assisted particle assembly (CAPA) and two-photon polymerization direct laser writing (2PP-DLW) to realize a new class of multi-material microstructures. We use 2PP-DLW both to fabricate 3D templates to guide the CAPA of soft- and hard colloids, and to link well-defined arrangements of functional micro-particle arrays produced by CAPA, a process we term "printing on particles". The printing process is based on automated particle recognition algorithms and enables the user to connect colloids into one-, two-, and three-dimensional tailored structures, via rigid, soft or responsive polymer links. Once printed and developed, the structures can be easily harvested and re-dispersed in water. We report particle clusters and lattices of varying symmetry and composition, and fabricate thermo-responsive micro-actuators and magnetically-driven "micro-machines", which can efficiently move, capture and release DNA-coated particles in solution. The flexibility of our method allows the combination of a wide range of functional materials into complex structures, which we envisage will boost the realization of new systems and devices for a broad range of fields, including microrobotics, micromanipulation and metamaterials. This article is protected by copyright. All rights reserved.
    Keywords:  additive manufacturing; assembly; colloids; hybrid materials; nanolithography
    DOI:  https://doi.org/10.1002/adma.202207101
  9. ACS Nano. 2023 Jan 04.
      The development of nanosystems with intrinsic immunomodulatory effects on macrophage polarization is important for the macrophage-targeted immunotherapy. Here, mitochondria-targeted bovine serum albumins (BSAs) via the conjugation of fluorescent, lipophilic, and cationic rhodamine 110 molecules can efficiently enhance the gene expression of the proinflammatory phenotype of macrophages and correspondingly inhibit the gene expression of their anti-inflammatory phenotype. On this basis, porous silicon nanocarriers can further boost the immunomodulation of these mitochondria-targeted BSAs in vitro or in vivo, accompanied by the secretion of proinflammatory mediators including tumor necrosis factor α, nitric oxide, and reactive oxygen species (ROS). Meanwhile, BSA coatings can also improve the biocompatibility of porous silicon nanoparticulate cores on macrophages. Finally, the mechanism investigations demonstrate that porous silicon nanocarriers can efficiently deliver mitochondria-targeted BSA into macrophages to generate mitochondrial ROS via the interference with mitochondrial respiratory chains, which can further trigger the downstream signaling transduction pathways for the proinflammatory transition. Considering the good biosafety and versatile loading capability, this developed porous silicon@BSA nanosystem with a strong proinflmmatory regulatory effect has important potential on the combinatorial chemoimmunotherapy against cancer or viral/bacterial-related infectious diseases.
    Keywords:  albumin proteins; macrophage polarization; mitochondrial targeting; porous silicon nanoparticles; reactive oxygen species (ROS); signaling transduction pathways
    DOI:  https://doi.org/10.1021/acsnano.2c07439
  10. Adv Healthc Mater. 2023 Jan 01. e2202409
      Fungal hyphae deeply invade the cornea in fungal keratitis. The corneal stroma hinders the infiltration of antifungal drugs and reduces their bioavailability. Here we report a peptide conjugate nano-assembly that permeates the stroma and kills the pathogen without irritating the ocular cornea. The hydrophilic surface of the nano-assembly ensures deep permeation into the stroma. When encountering a fungal hyphal cell, the nano-assembly disassembles and exposes the α-helical peptide to destroy the fungal membrane, thus inactivating the pathogen. In a rabbit model of fungal keratitis, the nano-assembly exhibits a better therapeutic effect than commercially available natamycin ophthalmic suspension. Peptide conjugates with a nano-assembled structure and assembly-disassembly behavior could serve as the foundation of a new therapy for fungal keratitis. This article is protected by copyright. All rights reserved.
    Keywords:  fungal keratitis; hyphae; peptide conjugate nano-assembly; stroma
    DOI:  https://doi.org/10.1002/adhm.202202409