bims-barned Biomed News
on BBB and Neurodegeneration-ALS
Issue of 2026–11–01
eighty-two papers selected by
Luca Bolliger, lxBio



  1. ChemMedChem. 2026 Nov 12. pii: e70554. [Epub ahead of print]21(21):
       BACKGROUND: Boron (B), a group 13 metalloid, has emerged as a versatile element at the intersection of chemistry, biology, and medicine. Its electron-deficient nature and ability to reversibly interconvert between trigonal planar (sp2) and tetrahedral (sp3) geometries enable dynamic covalent interactions with biological nucleophiles, making boron-containing compounds (BCCs) attractive pharmacophores that selectively interact with reactive oxygen species (ROS) and are ROS-responsive for therapeutic development. BCCs possess antioxidant, anti-inflammatory, and metal-chelating properties that make them attractive candidates for neurodegenerative diseases. Amyotrophic lateral sclerosis (ALS), a fatal and multifactorial motor neurodegenerative disorder, is characterized by oxidative stress, neuroinflammation, mitochondrial dysfunction, and metal dyshomeostasis, providing a strong rationale for exploring boron-based therapeutics.
    METHODS: This review examines current literature on B chemistry, pharmacology, and translational applications, with emphasis on mechanisms relevant to ALS pathogenesis. This review focuses on ROS-responsive B scaffolds, blood-brain barrier (BBB) permeability, neuroprotective mechanisms, hormonal modulation, metal chelation, and emerging preclinical evidence supporting boron-based interventions.
    CONCLUSIONS: BCCs represent a promising yet underexplored therapeutic platform for ALS and related neurodegenerative disorders. Their ROS-responsive, redox-modulating, and neuroprotective properties, combined with favorable CNS drug-like pharmacokinetics, offer a mechanistically distinct approach to disease modification. Emerging preclinical evidence strongly supports further translational investigation.
    Keywords:  amyotrophic lateral sclerosis (ALS); blood–brain barrier (BBB); boron (B); boron‐containing compounds (BCCs); neurodegeneration; reactive oxygen species (ROS)
    DOI:  https://doi.org/10.1002/cmdc.70554
  2. Int J Mol Sci. 2026 Oct 13. pii: 9084. [Epub ahead of print]27(20):
      Amyotrophic lateral sclerosis (ALS) is a rapidly progressing neurodegenerative disorder that selectively affects motor neurons. The median survival time after diagnosis is 2 to 5 years. Oxidative stress (OS), driven mainly by reactive oxygen species (ROS), plays a central role in motor neuron (MN) degeneration. In this narrative review, we analyse the pathogenic role of SOD1 variants and their contribution to OS in ALS. SOD1 mutations alter the Cu/Zn superoxide dismutase enzyme, thereby promoting oxidative damage and triggering neuroinflammatory cascades via the MAPK, NF-κB and Nrf2/ARE signalling pathways. We also discuss emerging proteomic and machine-learning biomarkers, as well as the current therapeutic landscape. Riluzole and edaravone are approved treatments, while AMX0035 was approved in 2022 but withdrawn in 2024. Masitinib and EPI-589 remain investigational. In the realm of genetic therapies, the antisense oligonucleotide tofersen received accelerated FDA approval in 2023 for SOD1-ALS, primarily due to its ability to reduce plasma neurofilament light chain levels. However, the clinical benefit remains modest. RNA interference has reached human trials, while CRISPR/Cas9 remains in the preclinical stage. Both approaches have shown promising results in experimental models. Further research into ALS pathogenesis is needed to develop treatments that integrate antioxidant, anti-inflammatory, and gene-editing strategies.
    Keywords:  ROS; SOD1; gene therapy
    DOI:  https://doi.org/10.3390/ijms27209084
  3. Cureus. 2026 Sep;18(9): e117043
      Amyotrophic lateral sclerosis (ALS) is characterized by prion-like propagation of misfolded TAR DNA-binding protein 43 (TDP-43) and superoxide dismutase 1 (SOD1) across motor neuron pools. Because any circulating pharmacological agent must cross the blood-brain and blood-spinal cord barriers (BBB and BSCB), this review proposes active craniospinal tensioning (ACT) as a mechanical, non-pharmacological route to disease modification that acts on cerebrospinal fluid (CSF) and venous pressure dynamics rather than requiring penetration of these barriers. ACT is proposed to engage a single Monro-Kellie/Queckenstedt pressure continuity through two concurrent mechanisms: suboccipital venous occlusion-rebound, hypothesized to transiently raise and release craniospinal CSF pressure via venous compression and thereby accelerate venous-side glymphatic efflux; and dural pull-recoil, hypothesized to generate a reciprocal CSF pressure gradient via spinal elongation, agitating perivascular CSF directly while inducing a coupled venous pressure gradient. Because both mechanisms act concurrently on a shared venous-side target, the combined maneuver is proposed to be more potent than either delivered alone, as in prior work on pelvis-stabilized axial spinal traction (PSAST), which lacks the occlusion-rebound component. A secondary, hypothesis-generating micro-biochemical axis, cerebral venous preconditioning (CVPC), proposes that the same occlusion-rebound cycle produces capillary/venule wall strain sufficient to activate heat shock factor 1 (HSF-1) across the neurovascular unit, independent of oxygen tension, with a possible but uncharacterized contribution from hypoxia-inducible factor 1-alpha (HIF-1α). The two routes are non-exclusive, with the macro-fluidic axis alone proposed as sufficient. This framework is entirely theoretical, requires preclinical and clinical validation, and is intended as a template for related proteinopathy-driven neurodegenerative diseases, including Parkinson's disease, Huntington's disease, spinocerebellar ataxia, and fatal familial insomnia, addressed in forthcoming work.
    Keywords:  active craniospinal tensioning (act); amyotrophic lateral sclerosis (als); blood-cns barrier (bcnsb); cerebral venous preconditioning (cvpc); dural pull-recoil; glymphatic-lymphatic clearance; heat shock factor 1 (hsf-1); sod1 proteinopathy; suboccipital venous occlusion-rebound; tdp-43 proteinopathy
    DOI:  https://doi.org/10.7759/cureus.117043
  4. Metab Brain Dis. 2026 Oct 24. pii: 246. [Epub ahead of print]41(1):
      The Wnt Signaling pathway is a regulatory network that is highly conserved in the central nervous system and is essential for the survival of neurons, synaptic plasticity, and the blood-brain barrier's integrity. The pathophysiology of major neurodegenerative and neurological disorders, including Alzheimer's disease (AD), Parkinson's disease (PD), Huntington's disease (HD), amyotrophic lateral sclerosis (ALS), and traumatic brain injury (TBI), is highly influenced by canonical and non-canonical Wnt Signaling dysregulation, according to increasingly compelling evidence. In addition to emphasising common molecular events such as GSK-3β overactivation, β-catenin destabilisation, neuroinflammation, synaptic dysfunction, and BBB disruption, this study offers a comparative and mechanistic overview of Wnt pathway changes across various illnesses. This article identifies overlapping treatment targets, such as GSK-3β, DKK1, LRP5/6, and Wnt ligands, by integrating common and disease-specific Wnt-associated pathways, in contrast to traditional disease-specific reviews. Furthermore, new translational approaches involving natural substances, Wnt modulators, and pathway-targeted treatments are critically examined. All things considered, this study presents Wnt Signaling as a potential neuroprotective and regenerative target for upcoming precision-based treatments in neurodegenerative disorders.
    Keywords:  Blood–brain barrier; GSK-3β; Neurodegenerative disorders; Neuroinflammation; Neuroprotection; Wnt signaling; β-catenin
    DOI:  https://doi.org/10.1007/s11011-026-02006-4
  5. Amyotroph Lateral Scler Frontotemporal Degener. 2026 Oct 28. 1-11
      Background: Amyotrophic lateral sclerosis (ALS) has been associated with thromboembolic risk. However, whether dynamic coagulation-fibrinolysis markers provide prognostic information in ALS remains insufficiently defined. Methods: We conducted a prospective cohort study of 151 patients with ALS, including repeated coagulation measurements in a longitudinal subset (n = 58), and assessed directional validation in the independent Answer ALS (AALS) cohort (n = 270). Survival analyses, longitudinal modeling, and plasma proteomic analyses were used to examine associations between coagulation-fibrinolysis dynamics, functional decline, and survival. Results: Higher baseline fibrinogen (FIB) was independently associated with shorter survival (HR = 2.19; 95% confidence interval (CI), 1.40-3.44). In the longitudinal subset, a steeper increase in D-dimer (DD) was associated with shorter survival (HR = 1.012; 95% CI, 1.001-1.024) and lower ALSFRS-R scores over time (β = -0.013; 95% CI, -0.016 to -0.009). Directionally consistent validation was observed in AALS using rescaled SomaScan-derived DD trajectories (HR = 1.0002; 95% CI, 1.0000-1.0004). Plasma proteomics showed reduced tetranectin, a fibrinolysis-related protein, in ALS; slower tetranectin decline was associated with longer survival using rescaled SomaScan-derived tetranectin trajectories (HR = 0.996; 95% CI, 0.993-0.998). Conclusions: These findings suggest that longitudinal coagulation-fibrinolysis markers may help identify a survival-related biomarker profile in ALS, involving higher baseline FIB, steeper rising DD, and reduced or more rapidly declining tetranectin.
    Keywords:  ALS; D-dimer; fibrinogen; survival; tetranectin
    DOI:  https://doi.org/10.1080/21678421.2026.2750602
  6. Brain Res. 2026 Oct 27. pii: S0006-8993(26)00480-4. [Epub ahead of print] 150618
      TAR DNA-binding protein 43 (TDP-43) pathology is a defining feature of amyotrophic lateral sclerosis (ALS) and frontotemporal dementia (FTD). Although TDP-43 dysfunction has traditionally been studied through a neuron-centric framework, increasing evidence demonstrates that astrocytes, microglia, and oligodendrocytes are also directly affected and actively contribute to disease progression. In this review, we examine how TDP-43 dysfunction disrupts lineage-specific glial homeostatic programs and promotes distinct pathological state transitions across major glial populations. In astrocytes, TDP-43 dysfunction impairs neurotransmitter regulation, metabolic and neuronal support, RNA homeostasis, and secretory signaling while promoting inflammatory and antiviral-like states. In microglia, altered TDP-43 disrupts inflammatory regulation, phagocytosis, lysosomal function, lipid metabolism, and stage-dependent protective responses. In oligodendrocytes, TDP-43 dysfunction compromises RNA processing, lineage maintenance, lipid metabolism, myelin integrity, and long-term axonal support. Together, these findings suggest that glial TDP-43 dysfunction cannot be reduced to a single generalized form of reactivity but instead reflects the breakdown of distinct cell type-specific identities required to maintain central nervous system homeostasis. A cross-glial framework integrating cell-autonomous dysfunction, non-cell-autonomous signaling, disease stage, and genetic context may therefore provide a more complete understanding of TDP-43 proteinopathy and its contribution to neurodegeneration across the ALS-FTD spectrum.
    Keywords:  Amyotrophic lateral sclerosis; Astrocytes; Frontotemporal dementia; Glia; Microglia; Oligodendrocytes; TDP-43
    DOI:  https://doi.org/10.1016/j.brainres.2026.150618
  7. Rinsho Ketsueki. 2026 ;67(9): 1145-1149
      Advances in induced pluripotent stem cell (iPSC) technology have enabled the establishment of patient-derived disease models, greatly accelerating research on disease mechanisms and drug discovery. Drug repositioning, which applies existing drugs to new indications, has emerged as an efficient therapeutic development strategy that reduces both development time and cost. This review summarizes recent progress in disease modeling and therapeutic research using iPSCs, focusing on amyotrophic lateral sclerosis (ALS). Motor neurons differentiated from ALS patient-derived iPSCs successfully recapitulated disease phenotypes and enabled compound screening. Using this platform, the Src/c-Abl inhibitor bosutinib was identified as a promising therapeutic candidate. Bosutinib promoted autophagy, reduced abnormal protein accumulation, and suppressed motor neuron degeneration in vitro and in vivo. Based on these findings, investigator-initiated clinical trials were conducted, demonstrating acceptable safety and suggesting potential efficacy in ALS patients. Furthermore, integration of iPSC-based analyses with biomarkers such as neurofilament light chain enabled patient stratification and suggested the feasibility of personalized therapeutic approaches. Future integration of iPSC models with artificial intelligence, genomic analysis, and real-world clinical data is expected to further enhance predictive precision and accelerate translational research. iPSC-based drug discovery therefore represents a promising platform for developing novel therapies for neurodegenerative diseases.
    Keywords:  Amyotrophic lateral sclerosis; Drug repositioning; Src/c-Abl pathway; iPSC-based drug discovery and development
    DOI:  https://doi.org/10.11406/rinketsu.67.1145
  8. Int J Mol Sci. 2026 Oct 21. pii: 9350. [Epub ahead of print]27(20):
      Amyotrophic lateral sclerosis (ALS) is a fatal neurodegenerative disorder characterized by marked genetic and phenotypic heterogeneity. Although pathogenic variants in major ALS genes, including C9ORF72, SOD1, TARDBP, and FUS, have provided fundamental insights into disease pathogenesis, many familial and most sporadic cases remain without a molecular diagnosis, suggesting a genetic architecture extending beyond coding variants and monogenic inheritance. Advances in genomic technologies have revealed contributions from deep-intronic and regulatory variants, structural rearrangements, repeat expansions, and other forms of genomic variation incompletely captured by standard diagnostic approaches. Evidence also indicates that combinations of rare variants with moderate or incomplete penetrance may contribute to disease susceptibility and clinical variability, supporting a multilayer model of ALS genetics. Population-specific variation and convergence of genetically diverse defects on common molecular pathways further complicate variant interpretation and disease classification. This review examines emerging components of ALS genetic architecture, including non-coding variation, structural variants, repeat expansions, oligogenic burden, ancestry-related gaps, and convergent neurodegenerative pathways. Integrating these genomic layers with functional and transcriptomic evidence may improve variant interpretation, diagnostic yield, patient stratification, and the development of mechanism-based precision therapies.
    Keywords:  amyotrophic lateral sclerosis; genetic architecture; non-coding variants; oligogenic inheritance; precision medicine; whole-genome sequencing
    DOI:  https://doi.org/10.3390/ijms27209350
  9. Neurobiol Dis. 2026 Oct 29. pii: S0969-9961(26)00415-8. [Epub ahead of print] 107669
       OBJECTIVE: To characterize the dynamics of plasma misfolded superoxide dismutase 1 (mSOD1) and evaluate its utility as a state-dependent biomarker for patient stratification and therapeutic monitoring in amyotrophic lateral sclerosis (ALS).
    METHODS: We utilized an SOD1/G93A mouse model and a cohort of 160 ALS patients, including four with SOD1 mutations, 12 with non-SOD1 mutations (C9orf72, TARDBP, FUS, OPTN), and 144 with nongenetic ALS. Chemical precipitation and enzyme-linked immunosorbent assay were used to quantify mSOD1 levels in plasma, spinal cord extracts, and cerebrospinal fluid (CSF). Clinical outcomes were assessed by the annual reduction in the revised ALS Functional Rating Scale (ALSFRS-R) score and ventilator-free survival.
    RESULTS: In mice, plasma mSOD1 increased at the late symptomatic stage with subsequent numerical decline at the humane endpoint, accompanied by progressive motor neuron loss and increasing mSOD1-associated pathology. In humans, mSOD1 was elevated in 100% of SOD1-mutant, 25% of non-SOD1-mutant, and 22.2% of nongenetic ALS patients. Elevation was state-dependent, enriched in patients with moderate disability (ALSFRS-R 17-45). Plasma and CSF mSOD1 levels were correlated across the overall ALS cohort, but this association was no longer significant after exclusion of SOD1-mutant ALS cases. In one tofersen-treated patient, plasma mSOD1 showed rapid, parallel, and sustained reduction with CSF levels. No significant differences in clinical outcomes were observed in nongenetic ALS based on mSOD1 status.
    INTERPRETATION: Approximately 22% of nongenetic ALS patients exhibit elevated plasma mSOD1, primarily during the moderate disease stage. Plasma mSOD1 is a candidate state-dependent biomarker for biological stratification and may have potential for treatment monitoring.
    Keywords:  Amyotrophic lateral sclerosis; Animal model; Misfolded superoxide dismutase 1 (SOD1); Motor neuron disease
    DOI:  https://doi.org/10.1016/j.nbd.2026.107669
  10. Res Involv Engagem. 2026 Oct 30. pii: 177. [Epub ahead of print]12(1):
       BACKGROUND: Amyotrophic lateral sclerosis (ALS) remains an incurable, progressive neurodegenerative disease. Patient and public involvement (PPI) has been increasingly recognized as a means to enhance the relevance, quality, and efficiency of research; however, its implementation in intractable neurological disease research remains limited in Japan. This webinar-based study, conducted through nationally advertised ALS Café events, aimed to clarify current PPI awareness among the Japanese ALS community and to explore strategies for promoting patient advocacy. Data were collected during the "ALS Café" held in September 2024 and a subsequent patient advocacy training program organized in October 2025. Among 79 respondents (42 patients with ALS and 37 caregivers), approximately 80% reported being unfamiliar with the concept of PPI, yet 72.2% expressed willingness to participate once the concept was explained. Among the 57 respondents willing to participate, interest was highest for involvement in translating research findings into practice (56.1%) and in identifying research themes (47.4%), and most (93%) stated that they expected no remuneration beyond reimbursement of expenses. The subsequent training program was well received, with mean evaluation scores exceeding 8.0 on a 0-10 scale, indicating high comprehensibility among participants (changes in knowledge or willingness to participate were not assessed). Respondents were a self-selected group of ALS Café participants with limited demographic characterization who may not represent patients and caregivers who do not participate in such events, and the training program evaluation lacked a pre-training baseline; these limitations should be considered when interpreting our findings.
    CONCLUSIONS: These findings reveal substantial stated willingness among Japanese patients with ALS and their caregivers to contribute to research despite low baseline awareness of PPI. This gap between limited awareness and high stated willingness suggests that targeted educational efforts could meaningfully expand patient engagement in ALS research. Systematic awareness-building initiatives, structured and accessible engagement opportunities, and sustained collaborative relationships between researchers and the patient community are essential for strengthening patient advocacy and accelerating drug development for ALS in Japan.
    Keywords:  Amyotrophic lateral sclerosis; Japan; Patient advocacy; Patient and public involvement; Patient engagement
    DOI:  https://doi.org/10.1186/s40900-026-01000-5
  11. Mater Today Bio. 2026 Dec;41 103738
      Complement-mediated glial inflammation and synaptic injury are increasingly implicated in amyotrophic lateral sclerosis (ALS), but clinically translatable complement-modulating therapies remain limited. Atovaquone (ATQ) is an approved, poorly water-soluble small molecule with reported immunomodulatory activity. We investigated whether ATQ could modulate C1qb or C5aR1-associated pathology and whether lactoferrin (Lf)-derived nanomicelles could improve delivery to the spinal cord. ALS spinal-cord single-cell transcriptomic and pathway-enrichment analyses were combined with screening of an FDA-approved drug library, molecular docking and surface plasmon resonance (SPR). Lf-ATQ nanomicelles were characterised by dynamic light scattering, transmission electron microscopy and fluorescence distribution studies. Complement/inflammasome responses were examined in microglial and motor-neuron-microglia models. Therapeutic effects were evaluated in mice expressing the human superoxide dismutase 1 G93A variant (SOD1G93A) by motor testing, compound muscle action potential recording, histology, immunostaining, western blotting and proteomics. Complement genes, particularly C1qb and C5aR1, were enriched in microglia, whereas glutamatergic-synapse and axon-guidance programmes were negatively enriched. In cellular models and SOD1G93A spinal cord, Lf-ATQ reduced C1qb, NLRP3 and multiple inflammatory mediators, attenuated glial reactivity and altered autophagy-related proteins. Treatment preserved rotarod performance, grip strength, gait parameters, compound muscle action potential amplitude and gastrocnemius morphology. Proteomic analysis indicated remodelling of complement/coagulation, vesicular-transport and synaptic modules. These findings support Lf-ATQ as a central nervous system (CNS) -oriented, complement-regulating nanotherapy candidate for ALS. Direct functional target-inhibition assays, quantitative ATQ pharmacokinetics, long-term safety assessment and validation in non-SOD1 models remain necessary before translational conclusions can be drawn.
    Keywords:  Amyotrophic lateral sclerosis; Atovaquone; C5aR1; Complement C1qb; Lactoferrin nanomicelles
    DOI:  https://doi.org/10.1016/j.mtbio.2026.103738
  12. Muscle Nerve. 2026 Oct 26.
       INTRODUCTION/AIMS: Phenotypic heterogeneity in amyotrophic lateral sclerosis (ALS) is an obstacle to stratification and survival prediction and is not sufficiently accounted for in clinical practice or trial design. We aimed to identify respiratory phenotypes to allow stratification and survival prediction in ALS.
    METHODS: We retrospectively analyzed 292 ALS patients. Data included demographics, disease-related characteristics, and respiratory measurements (initial predicted forced vital capacity [FVC] and 3-month decline slope). Survival analysis was performed using Kaplan-Meier estimates and Cox regression. We defined four respiratory phenotypes based on dichotomized predicted FVC at the initial visit and its 3-month decline slope: (1) initial high, slow decline (IHSD), (2) initial high, fast decline (IHFD), (3) initial low, slow decline (ILSD), and (4) initial low, fast decline (ILFD).
    RESULTS: Patients with an initial predicted FVC above the median had a median survival of 33 months, compared to 15 months for those below the median (p < 0.0001). The highest quartile had an almost threefold survival advantage over the lowest quartile (37 vs. 13 months, p < 0.0001). A 3-month slope at or above the median predicted longer survival (33 vs. 14 months, p < 0.0001). Survival varied across respiratory phenotypes, ranging from 41 months in IHSD to 11 months in ILFD-with all comparisons being significant (p ≤ 0.0012) except for ILSD vs. IHFD.
    DISCUSSION: Defining respiratory phenotypes in ALS may allow tailored research within those subgroups, biomarker correlations, more accurate prognostication, and stratification in clinical trials based on phenotype-specific disease progression.
    Keywords:  ALS; disease progression; prognostication; respiratory function; stratification
    DOI:  https://doi.org/10.1002/mus.70443
  13. Cells. 2026 Oct 16. pii: 1890. [Epub ahead of print]15(20):
      Amyotrophic lateral sclerosis (ALS) kills within a few years of onset, and the drugs licensed for treatment change that course only marginally. Silencing SOD1 has become a credible treatment route, but two gaps hold this approach back: an efficient vector platform for spinal cord transduction with limited peripheral transduction and evidence on whether adding neurotrophic support to gene silencing has any effect. We built an rAAV2-retro platform for intrathecal delivery. One intrathecal dose of an eGFP-expressing vector transduced all spinal cord segments and several brain regions, with a clear preference for spinal motor neurons and low expression in the liver and heart. Side by side in adult mice, we then used this platform to compare miRNA-mediated silencing of human SOD1, overexpression of IGF1, and the two together in SOD1G93A animals. A single injection of rAAV2-retro carrying an anti-hSOD1 miRNA extended median survival by 25 days, improved motor performance, protected neuromuscular junctions, spared α-motor neurons, and damped gliosis and apoptosis. IGF1 on its own also lengthened survival and limited neuronal loss, but it left motor performance unchanged. The benefit of IGF1 over miRNA alone was observed on most endpoints under the conditions tested; a modest, nominally significant improvement in hindlimb clasping was observed, which should be interpreted as exploratory given the number of comparisons performed. Silencing of hSOD1 therefore accounts for most of the benefit, and no statistically detectable additional benefit was observed for IGF1 on top of hSOD1 silencing under the conditions tested. A single intrathecal dose of rAAV2-retro-miRNA is thus an effective gene silencing approach in the SOD1G93A mouse model, with limited peripheral transduction in the liver and heart observed in C57BL/6J mice. However, these data also show the difficulty of achieving additional benefit by adding IGF1 under the conditions tested.
    Keywords:  IGF1; amyotrophic lateral sclerosis (ALS); miRNA; rAAV2-retro
    DOI:  https://doi.org/10.3390/cells15201890
  14. Neural Regen Res. 2026 Oct 24.
       ABSTRACT: Amyotrophic lateral sclerosis is a progressive neurodegenerative disease characterized by the degeneration of both upper and lower motor neurons. Recent advances in human-induced pluripotent stem cell-derived brain organoids offer an innovative platform to model amyotrophic lateral sclerosis in a human-specific context. These three-dimensional organoid systems allow for the study of neuronal circuit-level dysfunction, which is central to amyotrophic lateral sclerosis pathogenesis, by incorporating multiple neuronal subtypes and supporting glial populations. In particular, the integration of region-specific brain organoids into assembloid models has enabled the reconstruction of functional long-range projections and cortico-motor circuits, closely resembling human neural connectivity. This review summarizes the generation and application of human induced pluripotent stem cell-derived brain organoids for amyotrophic lateral sclerosis research, with a focus on the reconstruction of neural circuits, multi-omics profiling, and functional assays. We also discuss how organoid systems can be leveraged for drug discovery and personalized medicine in amyotrophic lateral sclerosis, highlighting their potential to unveil human-specific disease mechanisms. Lastly, we address the current challenges and future directions for improving the physiological relevance of organoid models in amyotrophic lateral sclerosis research.
    Keywords:  amyotrophic lateral sclerosis; assembloids; brain organoid; motor neuron disease; neural circuits
    DOI:  https://doi.org/10.4103/NRR.NRRONLINE-D-26-00781
  15. J Clin Med. 2026 Oct 14. pii: 7937. [Epub ahead of print]15(20):
      Background/Objectives: Adjuvant cell-based strategies are still being explored in amyotrophic lateral sclerosis (ALS). Materials and Methods: In this open-label, single-arm study of intrathecal autologous bone marrow-derived lineage-negative (LIN-) cells, we report functional status, quality of life, and survival after three administrations at six-week intervals. A total of 45 patients with sporadic ALS were qualified: 42 received all three administrations and 23 completed the 24-week assessment schedule, while 19 stopped attending because of deterioration. Results: In the 23 completers, Norris scale scores were stable until week 13 and then declined (p = 0.00004), and the Amyotrophic Lateral Sclerosis Assessment Questionnaire 40 (ALSAQ-40) followed the same pattern (p = 0.0019), whereas the ALS Functional Rating Scale-Revised (ALSFRS-R) declined at a constant 0.5 points per month. In all 42 treated patients the Norris score fell during treatment (0.95 points per month; 95% CI 0.52-1.38), so the plateau was confined to completers, who had milder baseline disease. Dose-related differences in quality of life were confounded by baseline imbalance; survival analyses were exploratory. Cell number did not correlate with cerebrospinal fluid brain-derived neurotrophic factor (BDNF) after the third administration in the 39 patients with paired samples (ρ = 0.14). No adverse event was recorded in 126 procedures, but harms were not graded systematically. Conclusions: These exploratory findings do not demonstrate efficacy; a sham-controlled trial with blinded raters is required.
    Keywords:  ALSAQ-40; ALSFRS-R; BDNF; Norris scale; amyotrophic lateral sclerosis; cell therapy; lineage-negative cells; quality of life; survival
    DOI:  https://doi.org/10.3390/jcm15207937
  16. Acta Neuropathol Commun. 2026 Oct 28. pii: 226. [Epub ahead of print]14(1):
      Accumulation of misfolded SOD1 protein into intracellular aggregates, in the spinal cord (SpC) and brainstem, is a hallmark of amyotrophic lateral sclerosis caused by mutations in the SOD1 gene (SOD1-ALS). Two distinct aggregate conformations, denoted strain A and strain B, were identified in the CNS of SOD1G85R and SOD1D90A transgenic (Tg) ALS mouse models, respectively. Both strains transmit templated SOD1 aggregation and ALS-like disease in Tg mouse models when inoculated into the SpC, whereas muscle or intraperitoneal inoculations, of up to 300 times more inoculate, did not. Here, we used strain A and strain B aggregate seeds, prepared from SpCs of the Tg mice, to investigate strain-specific differences in transmission of templated aggregation and ALS phenotype via a peripheral nerve. We show that both strains can transmit templated aggregation to the CNS via the sciatic nerve in SOD1G85R Tg mice. Strain A resulted in shorter time to disease onset and earlier end-stage disease compared to strain B, and these strain-specific differences were accentuated in the sciatic nerve inoculation model compared to direct SpC inoculations. To further analyse the differences between strain A and strain B, we developed an immunohistochemical method that distinguishes the two SOD1 aggregate strains in tissue sections. This method revealed that strain B adopts an elongated, skein-like morphology, whereas strain A aggregates appear as accumulations of rounded, bead-like structures. These findings suggest that SOD1 aggregates forming in a peripheral nerve might transmit disease to the CNS and that different SOD1 aggregate strains can influence disease onset and progression. Our results warrant further exploratory studies of SOD1 aggregate conformations and their potential role in the manifestation of SOD1 mutant-specific disease phenotypes.
    Keywords:  ALS; Aggregate conformation; Amyotrophic lateral sclerosis; Motor neuron disease; Neurodegenerative disease; SOD1; Sciatic nerve; Strain morphology; Templated aggregation
    DOI:  https://doi.org/10.1186/s40478-026-02455-z
  17. Int J Mol Sci. 2026 Oct 15. pii: 9157. [Epub ahead of print]27(20):
      Amyotrophic Lateral Sclerosis (ALS) is a rapidly progressing, fatal neurodegenerative disorder that selectively affects motor neurons. Clinical manifestations include progressive muscle weakness, amyotrophy, fasciculations, dysphagia, and fatal respiratory failure. The median survival after symptom onset is typically 2 to 5 years. Despite its severity, the epidemiological profile and genetic landscape of ALS in Latin American populations, particularly in Mexico, remain unclear. In this study, we evaluated the mutational spectrum of the SOD1 gene in a Mexican cohort of 156 ALS patients. Using high-resolution melting (HRM) analysis and Sanger sequencing, we identified 22 SOD1 variants in 42 of 156 patients (overall variant carrier frequency, 26.92%). Pathogenic or likely pathogenic (P/LP) variants were found in 21 patients (13.5%). Notably, 5 of the 22 variants were novel, expanding the spectrum of SOD1 variants. The variant carrier frequency identified in this study is higher than that reported for European populations but similar to frequencies observed in Asian populations. Our results highlight the distinct genetic heterogeneity of ALS in Mexico and demonstrate that HRM is a rapid and effective method for identifying SOD1 gene variants.
    Keywords:  Amyotrophic Lateral Sclerosis (ALS); Mexico; SOD1 gene; genetic variants; high-resolution melting (HRM); reactive oxygen species (ROS)
    DOI:  https://doi.org/10.3390/ijms27209157
  18. Int J Mol Sci. 2026 Oct 20. pii: 9322. [Epub ahead of print]27(20):
      Neurodegenerative diseases, including Alzheimer's disease (AD), Parkinson's disease (PD), and amyotrophic lateral sclerosis (ALS), are multifactorial disorders in which genetic susceptibility alone cannot account for sporadic onset, clinical diversity, or age-dependent progression. Epigenetic mechanisms-DNA methylation, histone modifications, non-coding RNAs, and m6A RNA methylation-bridge environmental and intracellular cues to stable gene expression changes. Emerging evidence associates epigenetic dysregulation with amyloid-β/tau pathology in AD, α-synuclein pathology in PD, and TDP-43/C9orf72-associated toxicity in ALS, while functional studies suggest that selected epigenetic alterations may contribute to these processes. In this narrative review, we distinguish associative, functional, and mechanistic evidence using claim-specific criteria based on experimental perturbation, direct molecular assessment, and pathway-dependence or rescue testing, while considering the study system. We further evaluate the translational promise of epigenetic biomarkers in liquid biopsies, while emphasizing the major barriers that separate bench findings from bedside application, including poor target specificity, limited blood-brain barrier penetration, and the absence of biomarker-guided patient stratification. By integrating pathological mechanisms, biomarker development, and therapeutic strategies, this review argues that future epigenetic research in neurodegeneration must prioritize causal validation, CNS-penetrant drug development, and prospective trials integrating epigenetic profiling to achieve meaningful clinical impact.
    Keywords:  DNA methylation; RNA methylation; epigenetics; histone modifications; neurodegenerative diseases; non-coding RNAs
    DOI:  https://doi.org/10.3390/ijms27209322
  19. Eur J Neurol. 2026 Nov;pii: e70798. [Epub ahead of print]33(11):
       BACKGROUND: Clinical heterogeneity in amyotrophic lateral sclerosis (ALS) may reflect structured disease trajectories. This study investigated whether anatomically defined motor phenotypes capture reproducible patterns associated with progression, serum neurofilament light chain (NfL), and survival.
    METHODS: In a multicenter cohort of 1307 ALS patients, motor phenotypes were classified by region of onset, timing of propagation to a vertically distant body region (early ≤ 12 months vs. later), and the degree of upper (UMN) and lower motor neuron (LMN) dysfunction. Intercenter consistency was assessed using the Friedman test and Kendall's W. Associations with ALS progression rate (ALSPR), NfL, and survival were analyzed using group comparisons and Cox regression models.
    RESULTS: Phenotype classification was consistent across centers (Kendall's W 0.75-0.89). Onset phenotypes were significantly associated with ALSPR, NfL, and survival (p < 0.001). Trunk onset showed the lowest log(NfL/ALSPR), indicating dissociation between rapid progression and relative NfL elevation. Early propagation was the strongest marker of disease aggressiveness, with higher ALSPR, elevated NfL, and reduced survival (HR 2.93, p < 0.001). In early propagation, NfL disproportionally increased with progression indicating a relative uncoupling of NfL from functional decline. Phenotypes with balanced UMN/LMN and predominant LMN involvement were associated with shorter survival (HR 2.51, p < 0.001).
    CONCLUSIONS: Anatomically defined motor phenotypes identify reproducible ALS trajectories with distinct clinical and neurofilament profiles. Early propagation provides an actionable risk marker of disease aggressiveness, while combined upper and lower motor neuron dysfunction or lower motor neuron predominance is prognostically unfavorable. These findings support integrating structured phenotyping into prognostic models and clinical trial stratification.
    Keywords:  amyotrophic lateral sclerosis; motor phenotypes; neurofilament light chain; propagation; survival
    DOI:  https://doi.org/10.1111/ene.70798
  20. Front Psychol. 2026 ;17 1960658
       Background: Mentalizing deficits are common in amyotrophic lateral sclerosis (ALS). Performance at high-level socio-cognitive tasks may be particularly vulnerable to integrity of basic cognitive processes. However, the extent to which non-social functioning contributes to socio-cognitive impairment in ALS remains poorly understood. In this study, we addressed this question in a large cohort of patients.
    Methods: We assessed 257 ALS patients and 120 healthy controls using the Story-based Empathy Task (SET), which dissociates intention attribution (IA), emotion attribution (EA), and basic causal inference (CI). Vectorial analyses were applied to quantify overall performance and imbalance between social and non-social components. Mediation analyses were conducted to evaluate the contribution of executive system integrity to social cognition performance in ALS.
    Results: Patients showed significantly reduced performance across all SET conditions compared to controls, with imbalance between mentalizing and basic causal inference. Distinct profiles emerged across ALS phenotypes. ALS patients with behavioral changes exhibited predominant deficits in emotion attribution, whereas cognitively unimpaired ALS showed selective impairment in intention attribution. Executive functioning was significantly associated with SET performances and mediated the relationship between basic inference and both intention and emotion attribution.
    Discussion: Mentalizing impairment in ALS reflects an interaction between executive processes and specialized socio-cognitive systems. The identification of dissociable profiles supports a dual-route, network-based model of ALS, involving socio-affective and inferential pathways, and underscores the importance of integrated cognitive assessment and more targeted interventions addressing both social and non-social cognitive domains.
    Keywords:  amyotrophic lateral sclerosis; executive deficits; mediation analysis; mentalizing; social cognition
    DOI:  https://doi.org/10.3389/fpsyg.2026.1960658
  21. Biomolecules. 2026 Oct 09. pii: 1470. [Epub ahead of print]16(10):
      Amyotrophic lateral sclerosis (ALS) is a progressive neurodegenerative disease characterized by the loss of motor neurons and widespread neural dysfunction. Loss of serotonin (5-HT) signaling and TAR DNA-binding protein 43 (TDP-43) dysfunction have both been identified as contributing factors to disease progression, although their relationship has yet to be fully defined. The objective of this review was to assess whether any mechanistic links exist between serotonergic dysfunction and TDP-43 proteinopathy in ALS. A scoping review was conducted in accordance with Preferred Reporting Items for Systematic Reviews and Meta-Analyses extension for Scoping Reviews (PRISMA-ScR) guidelines. Databases were queried for the peer-reviewed literature concerning ALS pathophysiology, 5-HT, and TDP-43 (1946 to January 2026). Articles were screened and data independently extracted by two reviewers, which were subsequently synthesized qualitatively (n = 14). The current literature suggests that serotonergic dysfunction can be identified early in ALS pathology, indicated by decreased 5-HT concentration, degeneration of raphe projections, and changes in receptor activity. TDP-43 proteinopathy is a defining characteristic of ALS progression, characterized by cytoplasmic mislocalization and aggregation of TDP-43. Additionally, studies have identified bidirectional links between these dysfunctions: TDP-43 impairs serotonergic transmission, and 5-HT deficiency may drive pathological TDP-43 aggregation. Many mechanisms affected by both serotonergic and TDP-43 dysfunction are associated with disease progression including excitotoxicity, metabolic disturbances, and network hyperexcitability. Despite this, there is a lack of direct experimental evidence elucidating connections between these pathologies. Serotonergic dysfunction and TDP-43 proteinopathy may be linked by shared mechanisms in ALS, though specific causality has not been identified. Further research should aim to clarify the connection between these processes and discover therapeutic targets.
    Keywords:  TAR DNA-binding protein 43 (TDP-43); amyotrophic lateral sclerosis (ALS); protein aggregation; serotonergic dysfunction; serotonin (5-HT); serotonin receptor (5-HTR)
    DOI:  https://doi.org/10.3390/biom16101470
  22. J Neurol. 2026 Oct 25. pii: 685. [Epub ahead of print]273(11):
       BACKGROUND: Amyotrophic lateral sclerosis (ALS) and frontotemporal dementia (FTD) are clinically and biologically related, and each may be preceded by a prodromal stage of disease. Mild cognitive and behavioural impairment (MCI/MBI) have also been observed in those with clinically manifest ALS. The primary aim of this study was to characterise MCI in presymptomatic ALS.
    METHODS: Criteria for frontotemporal-related MCI (MCI-ft), which require evidence of subthreshold cognitive performance or decline, were adapted from existing frameworks for MCI in prodromal FTD, presymptomatic ALS and clinically manifest ALS. MCI-ft was characterised in 216 Pre-fALS participants (74 C9ORF72, 94 SOD1, 20 other pathogenic variant carriers and 28 non-carriers) with neuropsychological data at 807 study visits. All designations were reviewed by a research neuropsychologist, with consensus discussions as needed.
    RESULTS: MCI-ft was observed in 15 (20%) C9ORF72, 12 (13%) SOD1 and 3 (%) of other carriers at one or more study visits, compared to 1 (4%) non-carrier. Most visits with MCI-ft showed impairment affecting both language and executive functioning. Fluctuations in MCI-ft status between assessments were common.
    CONCLUSION: The observed frequency and temporal course of MCI-ft in presymptomatic ALS, using criteria based on subthreshold cognitive performance and decline, expands understanding of this phase of disease. These findings help to inform future research examining the risk of phenoconversion to clinically manifest disease and aid the design of disease prevention trials.
    Keywords:  Frontotemporal dementia; Motor neuron disease; Presymptomatic disease; Prodromal symptoms
    DOI:  https://doi.org/10.1007/s00415-026-14206-0
  23. Brain. 2026 Oct 27. pii: awag375. [Epub ahead of print]
    Alliance Genetics Task Force Working Group Members
      Amyotrophic lateral sclerosis (ALS) is a progressive neurodegenerative disease with substantial clinical and genetic heterogeneity. Advances in ALS genomics, emerging gene-targeted therapies, and genotype-specific clinical trials have increased the importance of genetic counselling and testing for individuals with ALS and their families. However, access to these services remains highly variable globally due to disparities in healthcare infrastructure, laboratory capacity, specialist availability, and funding. Existing guidance has largely been developed in high-resource settings and may not be feasible or equitable worldwide. The International Alliance of ALS/MND Associations convened an international, multidisciplinary Genetics Task Force to develop expert consensus recommendations for genetic counselling, genetic testing, and laboratory practice in ALS across diverse geographic and resource settings. Recommendations were developed through a structured, iterative consensus process incorporating clinical expertise, lived experience perspectives, published evidence, and global representation. Final recommendations were reviewed and approved through anonymous voting at an in-person consensus meeting. The resulting recommendations establish both minimum and aspirational best practices, emphasizing equitable access, informed decision-making, culturally responsive counselling, tiered genetic testing approaches, and context-appropriate laboratory standards. These globally informed recommendations provide a pragmatic framework to support clinicians, laboratories, policymakers, and advocacy organizations in improving access to high-quality ALS genetics services worldwide.
    Keywords:  ALS; amyotrophic lateral sclerosis; best practice; genetic counselling; genetic testing
    DOI:  https://doi.org/10.1093/brain/awag375
  24. J Hum Genet. 2026 Oct 27.
      Traditionally conceptualized as a soma-centric pathology, amyotrophic lateral sclerosis (ALS) is a fatal, heterogeneous neurodegenerative disease. The suboptimal outcomes of central nervous system (CNS)-directed therapeutic strategies have necessitated a shift in focus toward the dying-back hypothesis. This hypothesis contends that synaptic disconnection and axonal retraction at the distal neuromuscular junction (NMJ) are early pathological events that may antedate overt motor neuron loss. This review systematically examines the NMJ as an early vulnerable and therapeutically tractable peripheral niche in ALS pathogenesis, rather than merely a downstream consequence of proximal proteinopathy. Evidence from human clinical samples and ALS mouse models, particularly SOD1-G93A mice, collectively supports the early vulnerability of the NMJ, with the temporal precedence of denervation, synaptic retraction, and mitochondrial dysfunction most clearly demonstrated in experimental models. We highlight how the breakdown of the tripartite synapse-comprising the motor terminal, skeletal muscle, and terminal Schwann cells (tSCs)-may disrupt essential neurotrophic signaling and local metabolic homeostasis. Furthermore, we discuss how advancements in humanized in vitro NMJ models and spatial transcriptomics provide unprecedented resolution into localized RNA dysmetabolism and bioenergetic failure. Finally, we evaluate emerging therapeutic strategies specifically designed to stabilize or restore the NMJ, including MuSK agonists and other NMJ-directed approaches. By recontextualizing the NMJ as a critical early site of vulnerability, we propose that targeting the peripheral synaptic microenvironment may offer a promising strategy for modifying the progression of ALS.
    DOI:  https://doi.org/10.1038/s10038-026-01522-6
  25. ChemMedChem. 2026 Oct 28. pii: e70539. [Epub ahead of print]21(20):
      Riluzole-derived benzo[d]thiazoles were investigated as metabolite-inspired CK1δ inhibitors, a kinase involved in TDP-43 phosphorylation and therefore relevant to amyotrophic lateral sclerosis (ALS). Starting from the known CK1δ activity of riluzole, we examined whether its major hydroxylamine metabolite could preserve target recognition and provide a rational entry point for scaffold optimisation. The metabolite retained CK1δ inhibition, but its limited chemical stability and toxicity in neuronal cells identified the hydroxylamine group as a critical liability. Replacement of this functionality with a hydrazine converted the fragile metabolite-derived structure into a more potent and tractable CK1δ inhibitor series. Structure-activity relationship studies revealed that the hydrazine moiety accommodates broader substitution than the hydroxylamine counterparts, with branched alkyl and benzyl groups giving the most balanced profiles. Docking and molecular dynamics suggested that the improvement could be attributed to an additional hydrogen-bond with Gly86 in the hinge region. The best derivative combined submicromolar CK1δ inhibition with passive blood-brain barrier permeability, short-term cellular tolerance, ATP competitive inhibition, direct target engagement, and preliminary selectivity over GSK3β. Although this compound did not result neuroprotective in an oxidative stress model, it paves the way for a focused benzo[d]thiazole platform for probing CK1δ biology in ALS.
    Keywords:  Casein kinase 1δ; benzo[d]thiazoles; lateral sclerosis; metabolism‐based drug design; riluzole
    DOI:  https://doi.org/10.1002/cmdc.70539
  26. PLoS Biol. 2026 Oct;24(10): e3004049
      The central problem when delivering drugs to the brain is no longer crossing the blood-brain barrier, but delivering therapeutics to the right cells, in the right regions to target neurodegeneration, within a dynamically changing neurovascular unit.
    DOI:  https://doi.org/10.1371/journal.pbio.3004049
  27. medRxiv. 2026 Oct 07. pii: 2026.10.06.26364580. [Epub ahead of print]
    French clinical and genetic research network on FTLD / FTLD-ALS PrevDemALS and STRATALS,
      Individuals carrying a G4C2 repeat expansion in C9orf72 can develop amyotrophic lateral sclerosis (ALS) and/or frontotemporal dementia (FTD), at various and unpredictable ages. The contribution of the expansion to this extreme clinical variability remained a matter of debate. In this work, we validated the use of optical genome mapping to efficiently size this expansion from blood and applied this method to a cohort of 54 repeat expansion carriers including patients with FTD (n = 23), ALS (n = 22) and presymptomatic individuals (n = 9). Despite the high variability in expansion profiles, distinct groups can be inferred. Although consensus repeat profiles were similar between FTD and ALS patients, relationships between repeat number, indexes of repeat instability, and the age at sampling differed between clinical conditions. An age at sampling-dependent increase of repeat instability in blood was observed in presymptomatic carriers and FTD patients (p = 0.01 and p = 0.04 respectively), in contrast to patients with ALS (p = 0.9). The proportion of shorter repeats ([500-1500 repeats]) increased with the age at sampling in ALS patients but decreased in presymptomatic and FTD cohorts, while the proportion of larger repeats (>2000 G4C2), in particular those exceeding 4000 repeats, increased along with the age at sampling in presymptomatic carriers and FTD cases (p <1.10 -e4 and p = 0.006 respectively) conversely to patients with ALS (p = 0.98). In conclusion, this work strongly supports different dynamics of repeat instability of the C9orf72 pathogenic expansion in blood linked to the clinical evolution. These findings provide new insights into the relationship between expansion profiles and clinical variability.
    DOI:  https://doi.org/10.64898/2026.10.06.26364580
  28. Acta Neuropathol Commun. 2026 Oct 27. pii: 225. [Epub ahead of print]14(1):
      Cytosolic aggregates containing misfolded superoxide dismutase-1 (SOD1) protein is an established hallmark of ALS caused by mutations in the SOD1 gene. We have previously identified two structurally distinct strains of human (h) SOD1 aggregates (denoted A and B) in mice transgenic (Tg) for hSOD1. Strain A and B have both been shown to transmit templated aggregation and induce early-onset of fatal ALS-like disease when injected directly into the spinal cord or peripheral nerve of hSOD1 Tg mice. In contrast, peripheral administration of hSOD1 aggregates into the intraperitoneal cavity or skeletal muscle did not induce disease. Collectively, these studies provide insight on the spreading mechanism of SOD1. However, the complete map of propagation routes and underlying mechanisms utilized by SOD1 aggregates in ALS is not fully charted. Here, we investigated whether hSOD1 aggregates may spread to the central nervous system (CNS) via the cerebrospinal fluid (CSF). Mutant hSOD1 aggregate seeds or control samples prepared from spinal cords of hSOD1 Tg mice or non-Tg mice, respectively, were inoculated into the cisterna magna of adult 100-day-old Tg mice expressing the G85R mutated hSOD1 protein. Disease phenotyping as well as biochemical and immunohistochemical analyses were performed and compared across the experimental groups. The mice inoculated with hSOD1 seeds developed early signs of ALS by 90 days after inoculation and reached terminal stage approximately 180 days earlier than mice receiving control seeds. Additionally, both strain A and B were observed to initiate templated aggregation along the neuroaxis. The results show that hSOD1 aggregates are capable of transmitting from the CSF to the CNS where they induce ALS-like pathology and concomitant phenotype. Unraveling the propagation pathways utilized by SOD1 opens new avenues to assess treatment strategies against ALS.
    Keywords:  Amyotrophic lateral sclerosis; Cerebrospinal fluid; Neurodegeneration; Prions; Superoxide dismutase-1
    DOI:  https://doi.org/10.1186/s40478-026-02473-x
  29. J Cachexia Sarcopenia Muscle. 2026 Oct;pii: e70411. [Epub ahead of print]17(5):
       BACKGROUND: Amyotrophic lateral sclerosis (ALS) is a devastating neuromuscular disease characterised by progressive muscle wasting and functional decline. Although cortical motor network disruption is a hallmark of ALS, the large-scale functional hierarchy alterations and their underlying molecular mechanisms in the early stage of the disease (ALS-ES) remain poorly understood. We aimed to characterise cortical gradient changes in early-stage ALS and to examine their neurochemical and transcriptomic correlates, as well as their cross-sectional associations with clinical functional status.
    METHODS: We recruited 97 patients with early-stage ALS, all at King's stage 1 and 94 healthy controls with comparable age and sex distributions. The ALS-ES group included 65 women and had a median ALSFRS-R score of 40 (IQR, 37-44). Resting-state fMRI was used to construct the principal functional gradient. We integrated neurochemical maps of 19 neurotransmitter receptors/transporters, and transcriptomic data from the Allen Human Brain Atlas. Partial least squares (PLS) regression and cell-type enrichment analysis were employed to identify molecular correlates of gradient alterations.
    RESULTS: Compared with HCs, ALS-ES patients exhibited a significant spatial contraction of the principal gradient. Specifically, gradient values significantly increased in the somatomotor network (SMN; t = 3.670, pFDR = 0.001) and decreased in the default mode network (DMN; t = -4.124, pFDR < 0.001). Within the ALS-ES group, higher SMN gradient values were associated with lower ALSFRS-R scores, whereas higher DMN gradient values were associated with higher ALSFRS-R scores. These macroscale alterations showed spatial correspondence with normative 5-HT4 receptor and norepinephrine transporter maps. PLS analysis identified a primary gene set (PLS1+) enriched in oligodendrocytes and mitochondrial functions (pFDR < 0.05), whereas the negative set (PLS1-) was associated with astrocytes, GABAergic neurons and RNA splicing pathways. Chromosome-level analysis revealed significant enrichment of PLS1- genes on chromosomes 5 and 16 (p < 0.05).
    CONCLUSIONS: Early-stage ALS is characterised by a collapsed cortical functional hierarchy centred on the motor-somatosensory axis. These alterations were spatially associated with normative neurochemical maps and distinct transcriptomic annotations related to energy metabolism and RNA processing. These findings identify cross-sectional cortical functional-hierarchy alterations associated with functional status in early-stage ALS and provide a multi-scale framework for investigating their neurochemical and transcriptomic correlates.
    Keywords:  Allen Human Brain Atlas; amyotrophic lateral sclerosis; cortical functional gradients; imaging transcriptomics; muscle wasting; neurotransmitter
    DOI:  https://doi.org/10.1002/jcsm.70411
  30. Naunyn Schmiedebergs Arch Pharmacol. 2026 Oct 28.
      Amyotrophic lateral sclerosis (ALS) is a progressive and fatal neurodegenerative disorder characterized by the selective degeneration of upper and lower motor neurons, resulting in progressive muscle weakness, paralysis, and respiratory failure. Despite the availability of disease-modifying therapies, current treatment options provide only modest clinical benefits, highlighting the need for novel therapeutic strategies targeting multiple pathological mechanisms. Melatonin, a pleiotropic neuroprotective molecule with antioxidant, anti-inflammatory, and anti-apoptotic properties, has emerged as a promising candidate; however, its influence on glucagon-like peptide-1 (GLP-1)-associated neuroprotective signaling and related molecular events in ALS remains poorly understood. Therefore, the present study investigated the neuroprotective efficacy of melatonin in a methylmercury (MTMR)-induced rat model of ALS and explored its effects on GLP-1-associated molecular alterations, neuroinflammation, oxidative stress, apoptosis, neurotransmitter homeostasis, demyelination, and neuronal injury. Molecular docking analysis was performed to predict the interaction of melatonin with proteins implicated in ALS pathology. Adult Wistar rats were exposed to MTMR (5 mg/kg, p.o.) for 21 days to induce ALS-like neurodegeneration, followed by treatment with melatonin (5 or 10 mg/kg, i.p.), edaravone (3 mg/kg, i.p.), or their combination for an additional 21 days. Neurobehavioral performance, biochemical alterations, hematological parameters, molecular biomarkers, and histopathological changes were subsequently evaluated. MTMR administration produced profound motor deficits accompanied by reduced GLP-1 levels, neurotransmitter imbalance, increased neuroinflammatory and apoptotic markers, elevated neurofilament light chain (NEFL), skeletal muscle injury, methylmercury accumulation, and extensive myelin and neuronal damage. Melatonin treatment significantly attenuated these pathological alterations in a dose-dependent manner by increasing GLP-1 levels, improving antioxidant status, reducing inflammatory and apoptotic responses, restoring neurotransmitter balance, preserving myelin integrity, and improving neuronal morphology across multiple brain regions and the spinal cord. Molecular docking further predicted favorable interactions between melatonin and several proteins associated with ALS pathophysiology, supporting its potential as a multitarget therapeutic agent. In most outcome measures, combined treatment with melatonin and edaravone produced greater neuroprotective effects than either intervention alone. Collectively, these findings demonstrate that melatonin substantially attenuates methylmercury-induced ALS-like neuropathology through coordinated modulation of multiple pathological processes associated with neurodegeneration. Although the precise molecular mechanisms require further experimental validation, the observed restoration of GLP-1 levels together with improvements in oxidative stress, neuroinflammation, apoptosis, neurotransmitter homeostasis, and myelin integrity suggests that melatonin may represent a promising adjunctive therapeutic strategy for ALS.
    Keywords:  Amyotrophic lateral sclerosis; Demyelination; Edaravone; GLP-1; Melatonin; Methylmercury; Neuroinflammation; Neuroprotection; Oxidative stress
    DOI:  https://doi.org/10.1007/s00210-026-06009-x
  31. Eur J Transl Myol. 2026 Oct 23.
      Functional electrical stimulation-assisted cycling may be relevant in motor neuron disease, but its feasibility and safety in amyotrophic lateral sclerosis and primary lateral sclerosis remain unclear. The authors aimed to assess feasibility, apparent safety, and exploratory pre-post clinical changes of a three-week functional electrical stimulation-assisted cycling protocol in ambulatory inpatients with amyotrophic lateral sclerosis or primary lateral sclerosis. Fifteen patients were assessed; 11 were enrolled (5 ALS, 6 PLS) and received 15 supervised 30-minute FES-cycling sessions over three weeks in addition to conventional neuromotor rehabilitation. Bilateral eight-channel stimulation targeted quadriceps, tibialis anterior, hamstrings, and gastrocnemius during active or active-assisted cycling. Feasibility outcomes were enrollment, completion, tolerance, adverse events, and pre-post data availability. Clinical outcomes were analyzed descriptively. Eleven of 15 assessed patients were enrolled (73.3%; 5 ALS, 6 PLS). All enrolled participants completed the protocol, no adverse events were documented, and complete pre-post data were available. Exploratory outcomes showed favorable short-term changes in mobility, walking, strength, and spasticity. This protocol appears feasible and apparently safe in selected ambulatory inpatients. Findings are hypothesis-generating and support a prospective controlled feasibility trial before efficacy is tested.
    Keywords:  Amyotrophic lateral sclerosis; apparent safety; feasibility; functional electrical stimulation; neurorehabilitation; primary lateral sclerosis
    DOI:  https://doi.org/10.4081/ejtm.2026.16025
  32. Open Biol. 2026 Oct 07. pii: 260209. [Epub ahead of print]16(10):
      Rare variants in NEK1, encoding a serine/threonine kinase, are among the most consistently implicated genetic contributors to amyotrophic lateral sclerosis (ALS), reported in approximately 2-3% of cases. Yet, while recent studies have characterized the cell biological consequences of NEK1 loss-of-function, the biochemical effects of ALS-associated missense variants on kinase activity have not been directly investigated. This distinction is mechanistically important, because missense alleles encode mutant proteins rather than simply reducing protein dosage. Here, we provide the most comprehensive cell-based phosphoproteomic map of NEK1 phosphorylation to date, identifying 10 recurrent phosphorylation sites across independent expression and acquisition conditions. We experimentally assign pSer14, pThr156 and pSer418 as NEK1 autophosphorylation sites using kinase-dead controls, targeted extracted ion chromatogram analysis, phosphosite mutagenesis and phosphospecific antibodies. Leveraging activation-loop pThr156 as a read-out of NEK1 activity, we assessed nine ALS-associated missense variants spanning the major functional regions of the protein. Among catalytic-domain variants, R261C produced the most robust reduction in pThr156 autophosphorylation, R232C produced a smaller reduction, and R232H increased pThr156; the basic-region variant, A313T, also showed a smaller reduction. Structural modelling provides a mechanistic framework for understanding these variant-specific effects. Our study establishes the first activity-based framework for functional classification of NEK1 missense variants, and provides direct evidence that ALS-associated missense variants can alter NEK1 autophosphorylation through a mechanism distinct from simple haploinsufficiency. The phosphospecific antibodies, isogenic cell lines and curated phosphoproteomic datasets generated here provide a community resource for future studies of NEK1 regulation, variant interpretation and therapeutic target validation.
    Keywords:  NEK1 kinase; amyotrophic lateral sclerosis; autophosphorylation; motor neuron disease
    DOI:  https://doi.org/10.1098/rsob.260209
  33. Front Neurol. 2026 ;17 1823485
       Objective: Hybrid Assistive Limb (HAL) is a cyborg-type wearable robot that supports gait training based on the wearer's intended motion. This study aimed to evaluate the effects of HAL treatment on gait ability and quality of life (QoL) in patients with amyotrophic lateral sclerosis (ALS).
    Methods: Patients with an unsteady gait with the ability to walk ≥10 m with assistance from a caregiver and/or walker were included in this study. Patients underwent nine HAL treatment sessions (20-40 min per session), with no more than one session per day, over a period of at least 4 weeks. Gait ability was evaluated using the distance of the 2-min walk test (2MWT), and the speed (m/s), step length (m/step), and cadence (step/s) of the 10-m walk test. Both tests were performed without HAL assistance. QoL was evaluated using the 36-Item Short Form Health Survey.
    Results: We evaluated 30 patients who completed one course of treatment. To evaluate the effectiveness of HAL, a paired t- test was used for the results of one course. With one course of treatment, the 2MWT improved from 92.27 m (40.46) at baseline to 104.16 m (41.73) (p < 0.001). Regarding QoL, the mental component summary score was 55.35 (8.27) before HAL treatment, indicating relatively preserved mental QoL. There were no significant changes in QoL before and after treatment.
    Conclusion: Although no curative treatment exists for ALS, HAL treatment may provide short-term improvement in gait ability in patients with ALS. However, no significant changes in QoL were observed after one course of treatment.
    Keywords:  QoL; SF-36; amyotrophic lateral sclerosis; cyborg robot; gait ability; hybrid assistive limb
    DOI:  https://doi.org/10.3389/fneur.2026.1823485
  34. J Neurol Sci. 2026 Oct 25. pii: S0022-510X(26)00517-4. [Epub ahead of print]491 126235
       OBJECTIVE: To evaluate the cost-effectiveness of multidisciplinary clinic (MDC) care compared with standard general neurology care for adults with amyotrophic lateral sclerosis (ALS).
    METHODS: A cost-utility analysis was conducted using a state-transition Markov model with monthly cycles over a 10-year horizon from the U.S. payer perspective. Health states comprised King's stages 1, 2, 3, 4 A, 4B, and death. Disease progression, mortality, utility, and cost inputs were derived from published literature (2005-2026). Transition probabilities were based on longitudinal data from the Pooled Resource Open-Access ALS Clinical Trials and permitted non-sequential progression. MDC-associated survival benefit was applied to stage-specific mortality across all King's stages. No additional utility benefit was assigned to MDC, while MDC-specific multipliers were applied to outpatient, inpatient, and emergency department costs. Outcomes included quality-adjusted life-years (QALYs), costs, cost per life-year gained, and incremental cost-effectiveness ratios (ICERs). Uncertainty intervals (UIs) were derived from sensitivity analyses.
    RESULTS: MDC increased costs ($523,170 vs $378,171) and QALYs (0.73 vs 0.60), yielding 0.13 incremental QALYs (95% UI, 0.06-0.20) at an incremental cost of US$144,999 (95% UI, $53,784-$257,504). The ICER was US$1,158,673/QALY and cost per life-year gained was US$149,483. MDC was cost-effective in 0.1% of simulations at a willingness-to-pay threshold of $150,000/QALY.
    CONCLUSION: MDC improved survival and quality-adjusted survival but at substantially higher cost. Its ICER remained well above commonly used U.S. willingness-to-pay thresholds across sensitivity analyses, including alternative utility valuations. These findings highlight the distinction between clinical benefit and cost-effectiveness and quantify the long-term economic consequences of survival gains associated with multidisciplinary ALS care.
    Keywords:  Amyotrophic lateral sclerosis; Cost-utility; Economic evaluation; Multidisciplinary clinics; Quality of life; Value
    DOI:  https://doi.org/10.1016/j.jns.2026.126235
  35. Ann Neurol. 2026 Oct 27.
       OBJECTIVE: The ALS Functional Rating Scale-Revised decline rate compresses trajectory shape into a single number, potentially missing distinct phenotypes. We tested whether shape identifies phenotypes that rate does not distinguish, and whether post-hoc analysis recovers a hidden ultrarapid subgroup.
    METHODS: From the Piemonte and Valle d'Aosta register (2000-2022), we applied 2 models to 1,686 amyotrophic lateral sclerosis patients: a Gaussian mixture model (GMM; rate axis) and a latent-class mixed model (LCMM) with cubic splines (shape axis). Concordance, prognostic performance, calibration, and clinical utility were assessed at 24 months. External validation used the Emilia-Romagna register.
    RESULTS: The rate model identified 4 classes (GMM-Slow 31%, GMM-Inter-slow 46%, GMM-Inter-fast 17%, GMM-Catastrophic 6%; slopes -0.44 to -3.52 points/month); the shape model 4 (LCMM-SlowLinear 46%, LCMM-PlateauFall 23%, LCMM-LateDecline 15%, LCMM-RapidEarly 16%). Concordance was modest (kappa = 0.273). Adding shape to rate changed discrimination negligibly (C-index 0.761 vs 0.755), but separated subgroups within rate classes (within GMM-Catastrophic, 30.1 vs 12.0 months). LCMM-LateDecline combined moderate early decline with reduced respiratory reserve (median forced vital capacity 83.5%) and 22.7-month median survival. The combined model gave the greatest net benefit for the composite outcome. Of 945 patients excluded for sparse sampling, 367 were ultrarapid progressors with shorter survival than LCMM-RapidEarly; findings replicated in the Emilia-Romagna register.
    INTERPRETATION: Rate and shape describe partially overlapping aspects of the disease. LCMM-LateDecline, with moderate early decline yet occult respiratory compromise, is clinically challenging, and the 3-visit criterion hides over half of ultrarapid patients. Rate predicts the overall burden of progression, whereas shape predicts the timing of deterioration. ANN NEUROL 2026.
    DOI:  https://doi.org/10.1002/ana.78394
  36. Mater Today Bio. 2026 Dec;41 103752
      Peroxisomes couple hydrogen peroxide metabolism to lipid homeostasis, making their functions relevant to neurological disease and to the design of intracellular catalytic biomaterials. However, the strength of disease-specific evidence and the functions reproduced by current materials vary substantially. This narrative review distinguishes modified biological peroxisomes from artificial and biomimetic platforms and evaluates how patient-derived induced pluripotent stem cell (iPSC) models could support their development. We examine membrane chemistry, substrate permeability, enzyme retention, catalytic activity, cell targeting, blood-brain barrier transport, three-dimensional tissue penetration, and intracellular fate. We separate the established causal role of peroxisomal defects in primary peroxisomal disorders from associative or unresolved findings in Alzheimer's disease, Parkinson's disease, and amyotrophic lateral sclerosis. Kleefstra syndrome is discussed as a hypothesis-generating neurodevelopmental model, without assuming a primary peroxisomal defect. Published artificial-organelle studies establish selected catalytic and delivery capabilities, but do not validate the integrated patient-specific CNS therapeutic strategy proposed here. We therefore outline a staged evaluation framework that combines materials characterization with mechanistic controls, differentiated neural cultures, multicellular models, animal pharmacology, safety, and manufacturing assessment. Comparison with conventional antioxidant carriers, plasmalogen supplementation, and PPAR agonists should determine whether compartmentalized catalysis offers a measurable advantage. We provide a platform classification, a disease-resolved evidence hierarchy, and a set of controls and measurable endpoints intended to make peroxisome-inspired constructs comparable across studies. Clinical development will require evidence of disease-relevant benefit beyond ROS reduction and an acceptable therapeutic window.
    Keywords:  Artificial organelles; Biomaterials; CNS delivery; Kleefstra syndrome; Oxidative stress; Patient-derived iPSCs; Peroxisome engineering
    DOI:  https://doi.org/10.1016/j.mtbio.2026.103752
  37. bioRxiv. 2026 Oct 08. pii: 2026.10.06.757033. [Epub ahead of print]
      Sporadic disease accounts for about 90% of amyotrophic lateral sclerosis (ALS) cases, and its biological heterogeneity is a major contributor to the failure of trials that enroll patients under a single diagnosis. Because sporadic ALS lacks a shared genetic anchor, identifying biological signals is critical for effective patient stratification. We analyzed induced pluripotent stem cell-derived motor neurons from 619 AnswerALS participants using transcriptomics, proteomics, and whole-genome sequencing and identified CCT2 as the first single-gene marker of a molecular state within sporadic ALS, providing a measurable basis for trial enrollment according to biology. We first anchored the analysis in known ALS genotypes. C9orf72 and SOD1 motor neurons did not converge on a common signature but retained genotype-specific differences that bulk postmortem tissue compresses. Scoring 391 sporadic patients along three transcriptomic axes (bioenergetic stress, cell cycle, and inflammation) resolved three states. One state was marked by CCT2, a TRiC chaperonin subunit, which distinguished it from the quiescent state with an area under the curve of 0.892. CCT2 was also elevated at the protein level and associated with the rate of ALSFRS-R decline, although this association weakened after adjustment for culture composition. Upstream regulator analysis placed this state downstream of MYC and mTORC1 activation. No germline test across 360 whole genomes explained these states. Validation using Target ALS data showed that the relationship between CCT2 and the cell cycle program was also present in postmortem cortex enriched for layer 5b projection neurons.
    DOI:  https://doi.org/10.64898/2026.10.06.757033
  38. Brain Commun. 2026 ;8(5): fcag382
      Amyotrophic lateral sclerosis is increasingly recognized as a multisystem neurodegenerative disorder, and recent evidence suggests that the cerebellum may contribute to disease pathology, although cerebellar metabolic alterations have not previously been demonstrated in vivo. This study investigated cerebellar metabolic and structural changes using proton magnetic resonance spectroscopy (1H-MRS) and volumetric imaging. Thirty patients with amyotrophic lateral sclerosis (21 M, mean age 59.7 ± 7.6 years), 22 healthy controls (HC, 10 M, mean age 59.8 ± 9.6 years) and 16 individuals with hereditary spastic paraplegia type 4 (8 M, mean age 50.8 ± 12.5 years), a potential clinical mimic, underwent 3T MRI and 1H-MRS with a single-voxel positioned in the left cerebellar hemisphere. Patients with amyotrophic lateral sclerosis showed significant reductions in myo-inositol/creatinine (P = 0.01) and glutathione/creatinine (P = 0.005), compared with HC, together with selective volume loss in cerebellar lobules I-IV, V, VI, and Crus I. Among metabolites, glutathione/creatinine had the highest discriminative accuracy for amyotrophic lateral sclerosis versus both HC and spastic paraplegia type 4, with areas under the curve of 0.80 and 0.71, respectively. These findings reveal distinct cerebellar metabolic alterations in amyotrophic lateral sclerosis, providing further evidence for cerebellar involvement in disease pathology and highlighting cerebellar 1H-MRS as a potential adjunct to diagnostic evaluation.
    Keywords:  amyotrophic lateral sclerosis; cerebellum; glutathione; magnetic resonance spectroscopy; spastic paraplegia type 4
    DOI:  https://doi.org/10.1093/braincomms/fcag382
  39. Front Drug Deliv. 2026 ;6 1934025
      The blood-brain barrier (BBB) is an obstacle to effective therapy in neurological disease because it restricts drug access to the brain. Borneol, a lipophilic bicyclic monoterpene used in traditional Chinese medicine, has been associated with opposing effects on BBB function: barrier integrity restoration in ischaemic stroke models and barrier permeability enhancement in drug-delivery models. This mini-review evaluates whether these findings represent a true contradiction or a context-dependent pattern of BBB modulation. The impact of borneol treatment on the intact and damaged barrier was compared by aligning matched readouts within the physical and selective barrier phenotype categories. For example, physical barrier integrity measures explored ionic permeability, tight junction (TJ) organization and macromolecular leakage and selective barrier function measures assessed transcytosis and transport related outcomes. Molecular markers of endothelial state and extracellular matrix integrity were also compared. Across stroke models, borneol was consistently associated with improved barrier resistance, junctional structure preservation and reduced pathological leakage, with the major facilitator superfamily domain-containing protein 2a (Mfsd2a) and caveolin-1 (Cav-1)-mediated transcytosis representing the most clearly defined downstream mechanistic pathway. In delivery models, borneol was associated with transient TEER reduction, TJ protein (claudin-5) redistribution and enhanced tracer or payload passage, consistent with reversible barrier loosening. When these findings were compared through matched readouts, these differences became less contradictory and more conditionally structured. Overall, borneol is better understood as a context-sensitive modulator of BBB function rather than a uniformly barrier-opening or barrier-protective agent. However, translation remains limited by substantial heterogeneity in model, dose and timing, together with unresolved upstream mechanisms.
    Keywords:  blood-brain barrier; blood-tumour barrier; borneol; drug delivery; ischaemic stroke; permeability; recovery; transient
    DOI:  https://doi.org/10.3389/fddev.2026.1934025
  40. Biometals. 2026 Oct 28.
      Heavy metal exposure has emerged as a significant environmental contributor to neurodegenerative disease, and a substantial body of mechanistic evidence implicates microglia in the pathological cascades that follow. Lead, cadmium, arsenic, manganese, copper, cobalt, mercury, and zinc disrupt central nervous system homeostasis through multiple cellular targets, but the resident innate immune cells of the brain are well placed to translate these insults into sustained neuroinflammation. Evidence for this critical narrative review was assembled through a purposive search of PubMed, MEDLINE, and Google Scholar for mechanistically informative studies reporting glial endpoints, with reference lists searched by hand and no systematic protocol applied. This review synthesizes current understanding of how individual metals engage microglial signaling networks, with particular attention to oxidative stress, NF-κB activation, NLRP3 inflammasome assembly, MAPK cascades, and suppression of the Nrf2 antioxidant axis. We examine the phenotypic spectrum that extends well beyond the classical M1/M2 dichotomy, including disease-associated microglia, lipid-droplet-accumulating microglia, and interferon-responsive states, and consider how metal-specific signatures map onto these transcriptional programs. Manganese-driven inflammasome assembly, cadmium-induced mitochondrial impairment, lead-mediated disruption of calcium homeostasis, and mercury-evoked autophagic dysfunction are discussed as illustrative examples of mechanistic divergence within a common neuroinflammatory framework. Glial responses to metal mixtures, which better represent real exposure than single-element designs, are considered separately, and the evidence for greater-than-additive effects is appraised. Downstream consequences for astrocyte reactivity, blood-brain barrier integrity, synaptic remodeling, and neuronal viability are placed in the context of Alzheimer's disease, Parkinson's disease, and amyotrophic lateral sclerosis. Therapeutic avenues are appraised, including chelation, natural antioxidants, NLRP3 inhibitors, TREM2 modulation, and microglial replacement strategies. Methodological constraints, particularly the overreliance on BV-2 cells and acute high-dose exposure paradigms, are critically considered. The review concludes by identifying priorities for translational research, including longitudinal human cohort studies, single-cell transcriptomic profiling of metal-exposed microglia, and the development of region-specific exposure models that better reflect chronic environmental realities.
    Keywords:  Disease-associated microglia; Environmental neurotoxicology; Heavy metals; Microglia; NLRP3 inflammasome; Neurodegeneration; Neuroinflammation
    DOI:  https://doi.org/10.1007/s10534-026-00895-7
  41. Medicina (Kaunas). 2026 Oct 09. pii: 1948. [Epub ahead of print]62(10):
      Background and Objective: Radiologically isolated syndrome (RIS) is characterized by magnetic resonance imaging (MRI) findings suggestive of multiple sclerosis (MS) in individuals without a history of clinical demyelinating events. Increasing evidence indicates that structural brain abnormalities may be present in RIS before the development of overt neurological symptoms. However, most previous studies have employed cross-sectional designs, limiting the ability to characterize the temporal evolution of neurodegenerative changes. This study aimed to investigate longitudinal changes in global, regional, and lobar brain volumes in individuals with RIS using serial MRI examinations obtained at least six months apart. Methods: Patients with RIS who had undergone two 3 Tesla (3T) brain MRI examinations separated by an interval of at least six months were retrospectively identified. Three-dimensional (3D) T1-weighted MRI scans obtained at both time points were analyzed using the volBrain pipeline of the volBrain platform to quantify global, regional, and lobar brain volumes. Longitudinal volumetric changes were expressed as annualized percentage volume changes. The number of T2 lesions and total T2 lesion volume were additionally assessed, and their associations with longitudinal brain volume changes were investigated. Results: A total of 28 patients with RIS were included. After correction for multiple comparisons using the Benjamini-Hochberg false discovery rate (FDR) procedure, significant annual volume loss was observed in total brain volume (p = 0.043), total cerebrum volume (p = 0.033), right cerebrum volume (p = 0.033), left cerebrum volume (p = 0.044), total thalamic volume (p = 0.033), right thalamic volume (p = 0.047), and left thalamic volume (p = 0.043). No significant associations were observed between annualized brain volume changes and follow-up duration, total or regional T2 lesion counts, or total T2 lesion volume. Similarly, annualized brain volume changes did not differ significantly between subgroups defined according to MRI progression, the presence of gadolinium-enhancing lesions, or the presence of spinal cord lesions. Conclusions: Longitudinal volumetric analysis demonstrated progressive brain volume loss involving both global and regional structures in patients with RIS. These findings provide further evidence of measurable longitudinal structural brain changes in RIS before the development of clinically overt demyelinating disease. Larger longitudinal studies incorporating appropriate control groups are warranted to further characterize the temporal trajectory of volumetric changes in RIS.
    Keywords:  brain atrophy; brain volume; longitudinal MRI; multiple sclerosis; neurodegeneration; radiologically isolated syndrome; volBrain
    DOI:  https://doi.org/10.3390/medicina62101948
  42. Cells. 2026 Oct 16. pii: 1889. [Epub ahead of print]15(20):
      Despite the success of suppressive antiretrovirals, infection with human immunodeficiency virus (HIV) is associated with several comorbidities which include negative consequences to the central nervous system (CNS), where disruption of the blood-brain barrier (BBB) is a major underlying factor in the resulting chronic inflammation and contribution to the pathogenesis of neuroHIV. Currently, the use of cannabis and cannabinoid derivatives among persons living with HIV (PWH) is common. Despite perceived benefits, we have previously identified context-dependent effects of cannabis use, including its impact on vascular biomarkers. In this study, we used an in vitro polycellular BBB model with two different human cerebrovascular endothelial cell lines (hCMEC/D3 and HBMEC/ci18) to test the effects of cannabinoids and their receptors on barrier integrity and function in the context of the latent HIV brain environment, mimicked by the addition of conditioned media from HIV latently infected promonocytes. We found that the two brain endothelial cell lines had similar responses to HIV-conditioned media by increasing permeability to dextran and decreased expression of tight junction proteins. However, their response to cannabinoids, particularly via the cannabinoid receptor 2 (CB2R), was markedly different, with hCMEC/D3 cells showing improvement of BBB integrity by all measures, but HBMEC/ci18 cells showing no benefits or aggravation of damage. While the contrasting effects were not due to differences in cell viability or proliferation, differences CB2R-elicited baseline G protein-coupled receptor (GPCR) response thresholds between the two cell lines were significant, revealed by forskolin-induced cAMP levels that were 50-200-fold higher in hCMEC/D3 cells in comparison to HBMEC/ci18. This was correlated to higher baseline CB2R expression in hCMEC/D3, and was not an HIV-induced signaling defect in HBMEC/ci18. The CBD/THC-induced phosphorylation of p38 MAPK was also significantly stronger in hCMEC/D3 compared to HBMEC/ci18, was abrogated by a CB2R inverse agonist/antagonist. Motivated by the need to identify predictors of positive response to cannabinoids, our study suggests that CB2R levels and GPCR activation thresholds in cerebrovascular endothelium may be important candidate mechanistic biomarkers to be tested in primary cells, animal models, and longitudinal clinical cohorts, with the goal of distinguishing beneficial versus aggravating effects of cannabis to the BBB, particularly in the context of HIV.
    Keywords:  blood-brain barrier; cannabis; human immunodeficiency virus; latency
    DOI:  https://doi.org/10.3390/cells15201889
  43. Pharmaceuticals (Basel). 2026 Sep 25. pii: 1524. [Epub ahead of print]19(10):
      Background/Objectives: Blood-brain barrier (BBB) permeability prediction is important for central nervous system drug discovery. Many models rely mainly on chemical structure, omit transport information, and may report optimistic performance when related compounds occur across training and test sets without adequate leakage control. We developed MechBBB, a two-stage, transport-informed machine-learning framework that adds learned efflux, influx, and passive-permeability scores to conventional molecular features and evaluates their added value under explicit leakage control. Methods: In Stage 1, three LightGBM models were trained on separate efflux, influx, and passive-permeability datasets to generate transport-related scores. BBBP compounds were excluded from Stage 1 training by InChIKey matching. In Stage 2, a LightGBM classifier was trained on BBBP using a Murcko scaffold split with the three Stage 1 scores, ten physicochemical descriptors, and 2048-bit ECFP4 fingerprints. Performance was compared with a descriptor-plus-fingerprint baseline without transport scores. External evaluation used a strict B3DB set (n = 4080) with no InChIKey or nonempty scaffold overlap with BBBP and was performed without retraining, recalibration, or threshold adjustment. MechBBB was also compared with official SwissADME BOILED-Egg predictions on a chemically matched external subset. Results: On the BBBP scaffold test set, MechBBB achieved an AUROC of 0.932, an AUPRC of 0.983, an MCC of 0.737, and a balanced accuracy of 0.866. The AUROC improvement over the descriptor-plus-fingerprint baseline was small but statistically significant in the paired test (ΔAUROC = 0.0096; p = 0.0425). Scaffold-grouped cross-validation did not show a consistent ranking advantage from adding the Stage 1 scores. On strict B3DB, MechBBB achieved an AUROC of 0.894 and an AUPRC of 0.893, with no significant ranking advantage over the baseline. On the matched B3DB subset (n = 4043), MechBBB achieved higher accuracy (0.814 vs. 0.682), balanced accuracy (0.806 vs. 0.693), sensitivity (0.910 vs. 0.541), and MCC (0.631 vs. 0.401) than SwissADME BOILED-Egg, whereas BOILED-Egg had higher specificity (0.845 vs. 0.703). SHAP analysis identified TPSA, NumHDonors, and p_pampa among the leading contributors. Conclusions: MechBBB provides a leakage controlled and externally tested framework that combines competitive BBB permeability prediction with per-compound transport-related information. The Stage 1 scores produced a modest internal improvement but did not provide a consistent external ranking advantage, indicating that their main added value is transport-related context rather than a universal increase in predictive accuracy. MechBBB can be used to prioritize compounds for CNS drug discovery before experimental BBB testing and identify compounds that may warrant follow-up studies of passive permeability or active transport. The MechBBB web tool is freely available.
    Keywords:  BBB permeability prediction; CNS drug discovery; P-glycoprotein efflux; PAMPA permeability; blood brain barrier (BBB); machine learning; mechanism informed modeling; solute carrier transporters
    DOI:  https://doi.org/10.3390/ph19101524
  44. Gen Hosp Psychiatry. 2026 Oct 21. pii: S0163-8343(26)00204-5. [Epub ahead of print]103 204-212
       OBJECTIVE: To synthesize clinically distinct suicide-related outcomes in amyotrophic lateral sclerosis (ALS) and comparative suicide risk without pooling non-equivalent constructs.
    METHODS: We searched MEDLINE, Embase, Scopus, PsycINFO, the Virtual Health Library, and SciELO through March 17, 2026, and updated all searches for March 18 through October 9, 2026. We included observational reports of predefined suicide-related outcomes. Outcomes with at least 3 independent studies were pooled using random-effects generalized linear mixed models for proportions and a Hartung-Knapp model for comparative estimates. We used Joanna Briggs Institute tools and adapted GRADE.
    RESULTS: Twenty-eight reports representing 26 independent cohorts were included; 21 cohorts contributed quantitative data. Active suicidal ideation was 43% (23/53; 95% CI, 30%-58%) in an end-stage cohort and 14% (10/71; 95% CI, 7%-24%) in a general clinic cohort; these estimates were not pooled. Hypothetical consideration of assisted dying was 50% (95% CI, 41%-59%; I2 = 49%; 95% prediction interval, 21%-79%; 4 studies). Crude suicide mortality rates were 0.16 and 0.36 per 100 person-years in 2 cohorts. Three registry or administrative cohorts yielded a relative suicide-risk estimate of 4.6 (95% CI, 2.5-8.5; 95% prediction interval, 0.4-53.6). Certainty was low or very low.
    CONCLUSIONS: Suicide-related experiences in ALS are clinically distinct. Clinicians should clarify meaning, assess intent and immediacy, evaluate decision-making capacity and treatable psychiatric symptoms, and address palliative and psychosocial needs. A death wish or assisted-dying preference should not be assumed to indicate active suicidal intent.
    Keywords:  Amyotrophic lateral sclerosis; Assisted dying; Suicidal ideation; Suicide; Systematic review; meta-analysis
    DOI:  https://doi.org/10.1016/j.genhosppsych.2026.10.002
  45. Biochemistry (Mosc). 2026 Oct;91(10): 1822-1841
      Contrary to the classical paradigm of brain immune privilege, damage-associated molecular patterns (DAMPs) act as key mediators in the dialogue between CNS cells and the immune system, determining pathways of immune response development. This review examines the role of key DAMPs - calreticulin (CRT) and high-mobility group box 1 protein (HMGB1) - in the functioning of CNS under normal conditions and during the development of neuropathologies, particularly oncological and neurodegenerative processes. Under normal conditions, CRT and HMGB1 ensure functioning of the brain, acting as necessary effectors of neurogenesis and homeostatic plasticity. In neurooncology, exposure of CRT on the surface of dying cells and release of HMGB1 serve as powerful adjuvant signals for antigen-presenting cells, inducing immunogenic cell death (ICD). Particular attention is given to the mechanisms of passive HMGB1 release during various types of regulated cell death (apoptosis, necroptosis, pyroptosis, ferroptosis, cuproptosis), as well as to the role of redox modifications of the protein, which determine its pro-inflammatory, immunogenic, or tolerogenic properties. In neurodegeneration (Alzheimer's disease, Parkinson's disease, amyotrophic lateral sclerosis), excessive DAMP release exacerbates the development of chronic neuroinflammation, disrupts integrity of the blood-brain barrier (BBB), and forms a vicious cycle of pathological changes. Detection of CRT and HMGB1 in biological fluids or brain tissues has important prognostic potential, and regulation of their signaling pathways opens promising approaches for overcoming tumor resistance or inhibiting progressive neurodegenerative changes in the brain.
    Keywords:  HMGB1; brain tumors; calreticulin (CRT); damage-associated molecular patterns (DAMPs); immunogenic cell death (ICD); neurodegenerative diseases; regulated cell death
    DOI:  https://doi.org/10.1134/S0006297926601565
  46. Biomedicines. 2026 Oct 14. pii: 2333. [Epub ahead of print]14(10):
      Background: Amyotrophic lateral sclerosis (ALS) is still a global health challenge, as there is no effective treatment due to the inadequacy of conventional experimental platforms for comprehending pathogenic mechanisms and developing therapy. Objectives: This review details the recent progress and clinical utility of next-generation iPSC-derived 3D in vitro systems integrated with microfluidics, CRISPR-Cas9 gene editing, multi-omics readouts, and AI-based machine learning, which are emerging as transformative platforms for recapitulating key ALS pathological hallmarks. Methods: A literature search was performed using PubMed and Web of Science, including only English-language publications. All the published papers collected covered the period from January 2015 to June 2026. Results: Human induced pluripotent stem cell (iPSC) cerebral organoids, assembloids, and organ-on-a-chip technologies are revolutionizing research into ALS by providing a way to model the complex spatial organization, cellular heterogeneity, and neural network dynamics of the human brain. Moreover, recent bioengineering advancements enable the inclusion of functional neurovascular units, the integration of resident immune cells (microglia), and the use of 3D bioprinting to accelerate the functional maturation of age-related phenotypes. CRISPR-Cas9 genome editing, OMICS, and machine learning improve tools for studying ALS and identifying therapeutic targets. Conclusions: Novel cell culture models may bridge the gap between preclinical animal models and human clinical trials and reduce the duration and costs of translation. Future work is likely to integrate bioprinting with organ-on-chip microfluidics, CRISPR-based genetic editing, and multi-omics readouts to build increasingly faithful, patient-specific ALS models for both basic research and precision therapeutics.
    Keywords:  3D bioprinting; amyotrophic lateral sclerosis (ALS); assembloids; brain organoids; disease modelling; gene editing; induced pluripotent stem cells (iPSCs); organ-on-a-chip; translational medicine
    DOI:  https://doi.org/10.3390/biomedicines14102333
  47. MedComm (2020). 2026 Nov;7(11): e71090
      Neurodegenerative diseases are a growing cause of disability worldwide, particularly as populations age. Although these disorders differ in etiology and clinical presentation, advances in genetics, neuropathology, and biomarker research have identified shared disturbances in protein homeostasis, mitochondrial function, and immune regulation. These processes may contribute to selective neuronal vulnerability and neural circuit dysfunction. These findings are refining disease classification and diagnosis, yet effective disease-modifying therapies remain limited. Disease-specific abnormalities remain essential to clinical interpretation and treatment selection. Existing reviews often focus on individual disorders or isolated mechanisms, leaving the links between shared biology and disease-specific phenotypes insufficiently clear. We synthesize evidence on the epidemiology, risk factors, classification, and pathophysiology of Alzheimer's disease, Parkinson's disease, amyotrophic lateral sclerosis, Huntington's disease, frontotemporal dementia, Friedreich's ataxia, and multiple sclerosis. We compare their clinical manifestations and diagnostic approaches, including the evolving role of biomarkers, and critically assess established and emerging therapies. By distinguishing shared mechanisms from disease-specific abnormalities, we identify key translational gaps and explore how common biological disturbances may lead to distinct clinical trajectories. This cross-disease perspective may inform diagnostic reasoning, treatment development, and future comparative research.
    Keywords:  Alzheimer's disease; Parkinson's disease; amyotrophic lateral sclerosis; diagnosis; neurodegenerative diseases; therapeutics
    DOI:  https://doi.org/10.1002/mco2.71090
  48. Respirol Case Rep. 2026 Nov;14(11): e70792
      This case report describes a 44-year-old man with amyotrophic lateral sclerosis (ALS) and ineffective secretion clearance despite home use of mechanical insufflation-exsufflation (MI-E). He reported upper airway obstruction, respiratory discomfort and recurrent aerophagia during therapy. Dynamic assessments using transnasal flexible laryngoscopy and videofluoroscopy under different MI-E settings showed that upper airway responses were strongly influenced by inspiratory flow, pressure levels, expiratory time and cervical positioning. Higher inspiratory flow and pressure induced supraglottic closure and airflow diversion to the oesophagus. In contrast, lower inspiratory flow combined with reduced expiratory pressure and shorter expiratory time improved glottic opening, maintained airway patency and enhanced cough mechanics. Spontaneously adopted cervical extension optimized airflow and minimized oesophageal insufflation, whereas neutral alignment impaired cough efficiency. These findings emphasize the importance of individualized MI-E settings and patient-specific biomechanics in optimizing therapy in ALS.
    Keywords:  amyotrophic lateral sclerosis; bulbar insufficiency; mechanical insufflation‐exsufflation; transnasal flexible laryngoscopy; videofluoroscopy
    DOI:  https://doi.org/10.1002/rcr2.70792
  49. Front Pharmacol. 2026 ;17 1706211
       Objective: To assess the effectiveness of specific Traditional Chinese Medicine (TCM) therapies for Amyotrophic Lateral Sclerosis (ALS) using Bayesian network meta-analysis.
    Methods: PubMed, the Cochrane Library, EMBASE, Web of Science, and four Chinese databases up to 15th December 2024 was searched, including RCTs on adult Amyotrophic Lateral Sclerosis patients treated with TCM therapies (Chinese herbal medicine, preparations, non-pharmacological treatments) alone or combined with conventional treatments. Controls included no intervention, placebo, conventional treatments, or combinations. Primary outcomes were functional status (ALSFRS, ALSFRS-R, AALSS, m-Norris scales). Bayesian network meta-analysis compared treatment effects and calculated SUCRA values.
    Results: Thirty-five RCTs involving 27 TCM therapies were included. No significant differences in functional status or quality of life were found among TCM therapies, ICT, Riluzole alone, and Riluzole plus placebo. For functional status, Shenmai injection + ICT (SUCRA 0.735 for ALSFRS, 0.870 for ALSFRS-R), Jiweiling injection + placebo (SUCRA 0.868 for ALSFRS), Jiawei Sijunzi decoction alone (SUCRA 0.739 for ALSFRS-R), Acupuncture + rehabilitation exercises + Riluzole (SUCRA 0.928 for AALSS, 0.863 for m-Norris) and Shenzhe Jiangqi powder + placebo (SUCRA 0.860 for m-Norris) had the highest probabilities of being superior treatment. For quality of life, Thunder fire moxibustion + Riluzole and Jiweiling injection + placebo for ALSAQ-40 were favorable.
    Conclusion: Despite no significant differences in functional status among TCM therapies, ICT, Riluzole alone, and Riluzole plus placebo, Jiweiling injection, Shenmai injection, Jiawei Sijunzi decoction, and Shenzhe Jiangqi powder may be regarded as candidate preparations for ALS patients. Future research should focus on real-world data to explore long-term effects and practical benefits.
    Systematic Review Registration: https://inplasy.com/inplasy-2024-8-0050/, identifier INPLASY202480050.
    Keywords:  Bayesian network meta-analysis; Chinese herbal medicine; amyotrophic lateral sclerosis; indirect comparison; rare disease; traditional Chinese medicine
    DOI:  https://doi.org/10.3389/fphar.2026.1706211
  50. Muscle Nerve. 2026 Oct 29.
       INTRODUCTION/AIMS: Amyotrophic lateral sclerosis (ALS) results in respiratory muscle weakness causing hypoventilation, retention of carbon dioxide (CO2), and chronic hypercapnic respiratory failure. In this pilot study, we performed a 12-month assessment of daytime and home nocturnal CO2 to track respiratory progression, determine relationships with surrogate respiratory measures, and assess the impact of non-invasive ventilatory support.
    METHODS: Adults with forced vital capacity (FVC) less than 90% predicted secondary to ALS were recruited from two sites in the northeast US. Participants were followed up at standard visits every 3 months for up to five visits. Spirometry, functional scores, and patient-reported outcomes of dyspnea were recorded. Each visit included a 15-min, seated measurement of transcutaneous CO2 (PtcCO2) while in clinic, followed by 3 nights of home overnight PtcCO2 monitoring. Linear mixed-effects models were employed to describe the changes that occurred longitudinally and resulting from the initiation of non-invasive ventilation (NIV).
    RESULTS: Sixteen subjects were enrolled, with nine completing the full study. Strength and FVC declined over time, while daytime PtcCO2 remained stable. Five individuals demonstrated nocturnal hypercapnia that preceded FVC < 50% predicted normal. Transition to NIV was associated with a 7 mmHg decrease in nocturnal PtcCO2.
    DISCUSSION: Home nocturnal PtcCO2 assessment in ALS may identify respiratory insufficiency prior to FVC. Transcutaneous CO2 may play a role in the respiratory management of patients as a biomarker for hypoventilation risk and NIV titration. However, equipment availability and data quality limitations would benefit from professional assistance rather than independent in-home use.
    Keywords:  capnography; hypoventilation; remote monitoring; sleep; spirometry
    DOI:  https://doi.org/10.1002/mus.70432
  51. Acta Neuropathol. 2026 Oct 30. pii: 65. [Epub ahead of print]152(1):
      A major challenge for identifying a disease-modifying cure for Parkinson's disease (PD) is creating models resembling key features of the disease including resting tremor, bradykinesia, muscle rigidity and gait disturbances. In addition, PD patients often develop cognitive symptoms that are associated with pathology in neocortical areas. Initially, PD rodent models were generated primarily by chemical neurotoxins that induce an acute loss of dopaminergic neurons. Upon discovery of familial-PD-linked genetic mutations in the SNCA gene-encoding α-synuclein (αS)-mice carrying these mutations provided deeper insight into the pathologic role of this synaptic protein throughout the brain. αS transgenic mouse models stand out for their ability to develop intraneuronal lesions that are rich in αS phospho-serine 129, a histopathological signature of the human PD brain. Recent advances in αS protein biochemistry led to the generation of mice carrying strategic amplifications of familial-PD-linked αS mutants, resulting in more pronounced neurodegeneration and progressive phenotype development. Here we review advances of αS transgenic mouse model development with a focus on strategic mutations that may have greater potential for identifying underlying disease mechanisms than classical single-mutant and wild-type αS overexpressing mice. We also present how the mice are currently used in testing drug efficacy and target engagement for PD drug discovery and outline strategies for utilizing such mice in basic and translational research.
    DOI:  https://doi.org/10.1007/s00401-026-03112-4
  52. Ann Intensive Care. 2026 ;16 100183
       Background: Data on patients with amyotrophic lateral sclerosis (ALS) admitted to the intensive care unit (ICU) for acute respiratory failure are scarce, and early prognostic markers are lacking.
    Methods: We conducted a retrospective cohort study of consecutive patients with ALS admitted for acute respiratory failure to two ICUs of a tertiary referral center between 2016 and 2022. The primary outcome was 3-month mortality. Factors associated with 3-month mortality were assessed using multivariable Cox proportional hazards regression. Survival and functional outcomes were evaluated up to 12 months.
    Results: Among 139 patients [median age 66 (IQR 57-73) years, 61.2% being men], 109 (78.4%) patients presented with hypercapnia and 82 (59.0%) with hypoxemia (defined as PaO₂/FiO₂ ratio < 300) at ICU admission, with frequent overlap between both conditions. Non-invasive ventilation was used in 79.9% of patients, while 13.7% were intubated, and 2.2% underwent tracheostomy. Three-month mortality was 48.2%, increasing to 61.2% and 74.1% at 6 and 12 months respectively. In multivariable analysis, hypoxemia at ICU admission was independently associated with increased 3-month mortality (HR = 2.27, 95% CI: 1.28-4.01; P = 0.005), along with older age (HR=1.03 per year, 95% CI: 1.00-1.06; P = 0.035). Among patients alive at 3 months, a majority (79.2%) were living at home.
    Conclusion: ICU admission for acute respiratory failure in ALS is associated with substantial short-term mortality, consistent with the poor prognosis inherent to the natural history of the disease. Hypoxemia at admission identifies a subgroup at particularly high risk of death and may help inform early prognostic assessment and shared decision-making. However, patients who survive the acute ICU phase frequently achieve favorable short-term outcomes, with most living at home at 3 months.
    Keywords:  Acute respiratory failure; Amyotrophic lateral sclerosis; Intensive care unit
    DOI:  https://doi.org/10.1016/j.aicoj.2026.100183
  53. J Ginseng Res. 2026 Nov;50(6): 101149
       Background: Central nervous system (CNS) diseases remain therapeutic challenges due to complex pathology and poor drug penetration across the blood-brain barrier (BBB). Ginsenosides, the active components of Panax ginseng, possess multi-target neuroprotective properties but exhibit low bioavailability.
    Purpose: This review synthesizes current evidence on ginsenoside mechanisms and evaluates the role of nanotechnology in enhancing their delivery and efficacy for CNS disorders.
    Study design: A systematic search was conducted following PRISMA guidelines across PubMed, Web of Science, CNKI, and Google Scholar (2015-present). Included studies investigated ginsenosides in neurological disease models and nano-formulation strategies.
    Results: Ginsenosides modulate neuroinflammation, oxidative stress, apoptosis, and calcium homeostasis through pathways involving NF-κB, Nrf2, and Bcl-2/Bax. Nano-delivery systems-such as liposomes, polymeric nanoparticles, and biomimetic vesicles-significantly improve ginsenoside stability, BBB traversal, and brain-targeted accumulation. Functionalization with ligands (e.g., Angiopep-2) or cell membranes further enhances specificity and therapeutic outcomes in ischemic stroke, glioma, Alzheimer's disease, and spinal cord injury models.
    Conclusion: Nanotechnology-based delivery systems potently augment the neuroprotective potential of ginsenosides, offering a promising strategy for multi-target CNS therapy. Future efforts should focus on translational safety, scalable production, and clinical validation.
    Keywords:  Blood-brain barrier; Central nervous system disorders; Ginsenosides; Nano-delivery systems; Neuroprotection
    DOI:  https://doi.org/10.1016/j.jgr.2026.101149
  54. Nutrients. 2026 Oct 09. pii: 3304. [Epub ahead of print]18(20):
      Parkinson's disease (PD) is increasingly recognized as a heterogeneous neurodegenerative disorder with multiple clinical and pathological trajectories. In a subset of patients, α-synuclein pathology may begin in the gut and subsequently spread to the brain, a pathway most relevant to the proposed body-first subtype of PD. Tea catechins, particularly epigallocatechin-3-gallate (EGCG), can influence α-synuclein aggregation, oxidative stress, inflammatory signaling, and gut microbial ecology. Because their systemic bioavailability is limited, substantial amounts reach the intestine and undergo microbiota-dependent biotransformation. This review examines whether parent catechins and their microbial metabolites could modify intestinal processes relevant to α-synuclein misfolding and seeding. Evidence indicates that catechins are converted into phenyl-γ-valerolactones and lower-molecular-weight phenolic metabolites, while microbial amyloids such as curli can promote α-synuclein aggregation in experimental models. EGCG can also remodel α-synuclein assemblies, and catechin exposure can alter microbial and inflammatory phenotypes. However, direct evidence that catechin-derived microbial metabolites inhibit curli-α-synuclein cross-seeding or reduce enteric α-synuclein seeding remains limited. By distinguishing general neuroprotection from effects on aggregation, seeding, and disease modification, this review integrates current evidence and highlights the potential relevance of microbiota-dependent catechin metabolism to gut-origin α-synuclein pathology and body-first PD.
    Keywords:  body-first Parkinson’s disease; cross-seeding; curli; epigallocatechin-3-gallate; gut microbiota; gut-origin α-synuclein pathology; microbial metabolites; tea catechins; α-synuclein seeding
    DOI:  https://doi.org/10.3390/nu18203304
  55. Neurol Sci. 2026 Oct 27. pii: 890. [Epub ahead of print]47(11):
       BACKGROUND: The prognostic value of spinal cord lesions and cord atrophy for long-term disability in multiple sclerosis (MS) remains unclear in real-world cohorts.
    METHODS: We retrospectively analysed 223 patients with relapse-onset MS. The earliest pre-treatment spinal MRI was scored for lesion characteristics, gadolinium enhancement, and focal cord atrophy, assessed in 172 lesion-positive patients. Outcomes, referenced to one-year EDSS, included EDSS worsening (conventional magnitude criteria), incident EDSS ≥ 3 at last assessment, clinician-recorded progression independent of relapse activity (PIRA), and conversion to secondary progressive MS (SPMS). Firth-penalised logistic and Cox models were adjusted for baseline EDSS, age at diagnosis, and sex (logistic models also for disease duration).
    RESULTS: Cord lesions were present in 172 patients (77.1%), and all outcomes were more frequent in this group (EDSS worsening 39.5% vs 13.7%, incident EDSS ≥ 3 31.5% vs 6.1%, PIRA 22.7% vs 5.9%, SPMS conversion 15.1% vs 3.9%; all p ≤ 0.04). Lesion presence was associated with EDSS worsening (OR 3.56, 95% CI 1.55-9.21), incident EDSS ≥ 3 (5.31, 1.62-22.74), and PIRA (4.09, 1.17-20.43). Among lesion-positive patients, focal atrophy was associated with EDSS worsening (2.72, 1.22-6.23), incident EDSS ≥ 3 (5.59, 1.96-17.18), PIRA (3.66, 1.41-9.67), and SPMS conversion (HR 4.07, 1.69-9.82), with a graded pattern across lesion/atrophy status. Topographical features showed no consistent association.
    CONCLUSION: Spinal cord involvement was associated with every disability outcome examined, and among lesion-positive patients, visually assessed focal atrophy distinguished those with the worst course. The qualitative exposure, unconfirmed endpoints, and retrospective design make these findings hypothesis-generating; they support standardised prospective spinal imaging rather than individual prognostication.
    Keywords:  Atrophy; Disease progression; Magnetic resonance imaging; Multiple sclerosis; Spinal cord diseases
    DOI:  https://doi.org/10.1007/s10072-026-09484-5
  56. Cells. 2026 Oct 20. pii: 1910. [Epub ahead of print]15(20):
      This narrative review analyzes how myokines act as key links in communication between skeletal muscle and the brain, focusing on the impact of aging on this axis. Although the current literature links defects in this signaling pathway to sarcopenia, neurodegeneration, and cognitive decline, we still do not know exactly what role each molecule plays individually. Among the main gaps in our understanding are questions about how these substances are transported to the nervous system, what their specific receptors are, and what cause-and-effect relationship actually exists between losing muscle mass and developing neurological problems. In fact, in humans, it remains unclear whether myokines actually reach the brain in truly effective concentrations or whether their benefits are due more to peripheral metabolic, vascular, and inflammatory changes. Today, most of the mechanistic evidence comes from animal and cellular models, while observational studies predominate in humans. This is further complicated by uncertainties regarding the actual origin of these proteins in tissues, their passage through the blood-brain barrier, and their measurement in the blood, making it difficult to determine whether these proteins act as causes, consequences, or simply compensatory responses to aging and disease. On the other hand, although exercise remains the most robust tool for maintaining muscle health and protecting cognitive function, it is still unclear whether we could replicate those same benefits by isolating and stimulating specific myokines. The major challenge for the future is to develop human studies that combine standardized biomarkers with long-term monitoring of muscle function, cognition, and brain structure. Only then will we know whether this fascinating muscle-brain axis can move beyond being a promising hypothesis to become a real therapeutic target.
    Keywords:  ageing; myokines; neurodegeneration; sarcopenia; skeletal muscle–brain axis
    DOI:  https://doi.org/10.3390/cells15201910
  57. Cell Rep. 2026 Oct 29. pii: S2211-1247(26)01207-6. [Epub ahead of print]45(11): 118128
      Gastaldo et al.1 report that lowering ataxin-2 protects neurons from TDP-43 toxicity in amyotrophic lateral sclerosis by activating neuronal glycolysis and astrocytic cholesterol synthesis, not by reversing TDP-43-dependent molecular pathology. The downstream effectors, IDH1 and HMGCS1, thus emerge as candidate therapeutic targets.
    DOI:  https://doi.org/10.1016/j.celrep.2026.118128
  58. ChemMedChem. 2026 Oct 28. pii: e70545. [Epub ahead of print]21(20):
      Two advances have reshaped our understanding of α-synuclein (αSyn) in Parkinson's disease (PD). First, αSyn can assemble through liquid-liquid phase separation (LLPS) and related condensation pathways, forming condensates that mature into Lewy-body-like assemblies. Although conventional crowding-driven LLPS requires supraphysiological protein concentrations, membrane-templated surface condensation has been reported in vitro at ~10 nM, making this pathway plausible in the lipid-rich, electrically active enteric nervous system (ENS). Second, seeding-competent αSyn is detectable in blood before motor onset using seed-amplification assays. This review asks whether condensate-derived αSyn generated in the gut constitutes a blood-borne seed population that is systematically underrepresented by fibril-biased assays. We evaluate each step of the proposed pathway, including gut-specific LLPS triggers, release into and survival within the circulation, blood-brain barrier (BBB) traversal, and clinical detection, while distinguishing established evidence from indirect inference and testable hypotheses. Many of these questions are now experimentally accessible. Molecular rotors detect condensates through microviscosity rather than cross-β structure, condensate-stage modulators have emerged, and receptor-interception strategies such as bemcentinib provide opportunities for mechanistic interrogation. Together, these advances position chemical biology to determine whether condensate-derived seeds contribute to PD pathogenesis.
    Keywords:  blood–brain barrier; extracellular vesicles; gut–brain axis; hematogenous propagation; liquid–liquid phase separation; molecular rotors; α‐synuclein
    DOI:  https://doi.org/10.1002/cmdc.70545
  59. Int J Nanomedicine. 2026 ;21 625730
       Purpose: Autophagy dysfunction is a key contributor to Parkinson's disease (PD) pathogenesis, driving α-synuclein (α-syn) accumulation and progressive dopaminergic neurodegeneration. Although enhancing autophagic clearance of α-syn represents a promising therapeutic strategy, achieving controlled modulation of autophagic flux while maintaining neuronal viability remains challenging.
    Methods: A focused ultrasound (FUS)-enabled exosomal rapamycin delivery platform (EXO-RPM) was designed to modulate autophagic degradation in PD models. We systematically characterized their morphology, physicochemical properties, and environmental stability. In vitro studies assessed cellular uptake, cytotoxicity, autophagy induction, autophagic pathway modulation, and α-syn clearance. Subsequently, ultrasound-guided brain accumulation, behavioral recovery, brain immunofluorescence, and positron emission tomography (PET) imaging were evaluated in vivo. Finally, the biosafety of the nanoplatform was evaluated via histopathological and biochemical analyses.
    Results: Under optimized conditions, EXO-RPM achieved a high encapsulation efficiency of 90.14%. This platform exploits endogenous transferrin-transferrin receptor interactions for brain-targeted delivery, while FUS provides spatiotemporal control by transiently opening the blood-brain barrier (BBB) and thereby enhancing drug accumulation in the brain parenchyma. Following FUS-mediated delivery, EXO-RPM reduced α-syn aggregation and neuronal toxicity in parkinsonian models. Mechanistically, EXO-RPM treatment activated both macroautophagy and chaperone-mediated autophagy (CMA)-related pathways, thereby promoting autophagic degradation of pathological α-syn. These effects were accompanied by increased striatal dopamine levels and elevated [18F]FP-(+)-DTBZ uptake in VMAT2-positive synaptic vesicles, as revealed by PET, ultimately ameliorating MPTP-induced motor deficits in parkinsonian mice.
    Conclusion: These findings suggest that FUS-enabled exosomal delivery may provide a strategy for restoring autophagic homeostasis and mitigating α-syn-driven neurodegeneration, with potential relevance to PD and other protein aggregation-associated central nervous system (CNS) disorders.
    Keywords:  Parkinson’s disease; autophagy; blood-brain barrier; exosomes; focused ultrasound
    DOI:  https://doi.org/10.2147/IJN.S625730
  60. J Neurol Sci. 2026 Oct 25. pii: S0022-510X(26)00513-7. [Epub ahead of print]491 126231
       BACKGROUND: We examined whether amyotrophic lateral sclerosis (ALS) is associated with cytoskeletal and glial transcriptional patterns compatible with developmental pathway re-engagement, while recognizing that similar patterns may arise from injury responses and altered cell composition.
    METHODS: Postmortem RNA-sequencing data from the Target ALS Postmortem Tissue Core were analyzed using linear mixed-effects models accounting for repeated tissue samples within subjects. Models were adjusted for tissue source, age at death, sex, and postmortem interval. Composite scores represented Arp2/3 activity, SOX9/MEGF10 developmental-glial expression, and MYH10-associated transport imbalance.
    RESULTS: ALS was associated with increased Arp2/3 expression (β = 0.399, P = 8.26 × 10-9), SOX9/MEGF10 expression (β = 0.643, P = 4.28 × 10-6), MYH10 expression (β = 0.308, P = 0.000801), and MYH10-KIF5C transport mismatch (β = 0.121, P = 0.00537); all remained significant after false-discovery-rate correction. The MYH10-Arp2/3 contractility index was not significant (β = -0.0909, P = 0.107).
    CONCLUSIONS: ALS was associated with higher expression of selected cytoskeletal and glial genes in bulk postmortem tissue. These cross-sectional associations are compatible with, but do not demonstrate, developmental program reactivation, altered protein activity, or causation. Cell-resolved and functional studies are needed.
    Keywords:  Amyotrophic lateral sclerosis; Arp2/3 complex; Cytoskeletal remodeling; Embryonic development; MYH10
    DOI:  https://doi.org/10.1016/j.jns.2026.126231
  61. Biochemistry (Mosc). 2026 Oct;91(10): 1991-2000
      Neuroinflammation plays an important role in the pathogenesis of Parkinson's disease (PD), a widespread chronic neurodegenerative disorder. However, the dynamics of cytokine alterations in the brain during disease progression remain poorly understood. In this study, we investigated the levels of pro-inflammatory (IL-6, IL-17A, and IFN-γ) and anti-inflammatory (IL-4 and IL-10) cytokines in selected brain regions of transgenic A53T mice that express a mutant form of human α-synuclein and develop age-dependent pathological and behavioral abnormalities (a widely used model of PD). In young A53T mice (2- and 5-month-old), reduced emotionality was accompanied by elevated levels of the pro-inflammatory cytokines IL-6 and IL-17A in the striatum compared with age-matched control mice. In contrast, 10-month-old A53T mice exhibiting motor impairments showed reduced levels of IL-6, IFN-γ, and IL-4 in the striatum, together with increased IL-10 levels in the frontal cortex. Thus, age-dependent behavioral abnormalities in A53T mice were associated with distinct changes in the content of pro- and anti-inflammatory cytokines. The levels of all cytokines examined were altered in the striatum, whereas only IL-10 was significantly changed in the frontal cortex. No differences between A53T and control mice were detected in cytokine levels in the hippocampus. The observed spatiotemporal patterns of immune and inflammatory alterations may contribute to a better understanding of neuroinflammatory mechanisms underlying PD progression and may provide a basis for identifying potential biomarkers and therapeutic targets.
    Keywords:  Parkinson’s disease model; age; behavior; frontal cortex; hippocampus; neuroinflammation; pro- and anti-inflammatory cytokines; striatum; transgenic A53T mice; α-synuclein
    DOI:  https://doi.org/10.1134/S0006297926600614
  62. Neural Regen Res. 2026 Oct 29.
       ABSTRACT: Neurodegenerative diseases are characterized by the abnormal aggregation of amyloid-β, tau, and α-synuclein and have traditionally been viewed as disorders driven primarily by cell-autonomous processes within the central nervous system. Emerging evidence from in vitro, animal, and epidemiological studies suggests that neurodegeneration occurs within a systemic context in which peripheral organs, particularly the lung, serve as sources and modulators of central proteinopathy. The lung continuously encounters airborne pollutants, infectious agents, and inflammatory stimuli that perturb pulmonary proteostasis, trigger amyloid-like conformations of endogenous proteins, including surfactant protein C, and release cytotoxic, prion-like tau and amyloid-β from the pulmonary endothelium. This narrative review synthesizes evidence on pulmonary sources of misfolded proteins (bacterial and viral infections, fine particulate matter, ozone, diesel exhaust, surfactant protein mutations, and oxidative stress), molecular mechanisms driving misfolding and proteostatic collapse, candidate routes by which lung-derived aggregates reach the central nervous system (hematogenous transport with blood-brain barrier disruption, extracellular vesicle trafficking, vagal transmission, and peripheral immune cell trafficking), and proposed neurodegenerative consequences including tauopathy, amyloid-β deposition, microglial priming, synaptic loss, and cognitive decline. Emerging therapeutic strategies include immunomodulation, extracellular vesicle-targeted interventions, blood-brain barrier stabilization, and aggregation inhibitors. Current evidence distinguishes causal mechanistic data from epidemiological associations and hypothesis-generating observations. To date, no direct causal evidence in humans has demonstrated that lung-derived aggregates seed brain pathology; this framework is hypothesis-generating and intended to guide targeted experimental testing.
    Keywords:  amyloid-β; lung-brain axis; neuroinflammation; protein misfolding; tauopathy
    DOI:  https://doi.org/10.4103/NRR.NRRONLINE-D-26-00893
  63. Drug Des Devel Ther. 2026 ;20 611558
      Alzheimer's Disease (AD) is the leading cause of dementia worldwide, with a growing global burden and limited disease-modifying therapeutic options. The transmembrane receptor termed triggering receptor expressed on myeloid cells 2 (TREM2), which is mainly expressed by myeloid cells, has emerged as a target of interest in AD due to its role in modulating microglia functions, including cholesterol metabolism, phagocytosis of amyloid-beta (Aβ), inflammatory signaling, and innate immune neuronal protection. Genetic research has also shown that partial loss-of-function mutations in the TREM2 gene, particularly the R47H and R62H variants, substantially increase the risk of late-onset AD, further underscoring the therapeutic rationale for enhancing TREM2 signaling to combat the disease. Therapeutic strategies targeting TREM2 have exponentially increased in recent years, spanning monoclonal antibodies (mAbs) with distinct epitopes and mechanisms of receptor modulation, orally bioavailable small-molecule drugs capable of penetrating the blood-brain barrier (BBB), and upstream mechanisms targeting the shedding of the TREM2 ectodomain. Early clinical trials have revealed that target engagement does not translate directly into clinical benefit in patients, highlighting knowledge gaps in the timing of intervention, patient selection, dose optimization, and the complex dichotomy of TREM2 signaling, in which both insufficient and excessive activation may be detrimental to AD patients. Nonetheless, the continued advancement of therapeutics into clinical trials reflects the confidence in the underlying scientific rationale. This narrative review summarizes the current understanding of wild-type and variant TREM2 signaling in AD pathogenesis, evaluates the preclinical and clinical evidence supporting each class of TREM2-targeted therapeutic strategies, and discusses the challenges, emerging insights, and future directions that could shape the next generation of TREM2-based interventions for AD.
    Keywords:  Alzheimer’s disease; TREM2; microglia; myeloid cells; neuroinflammation
    DOI:  https://doi.org/10.2147/DDDT.S611558
  64. Respir Physiol Neurobiol. 2026 Oct 26. pii: S1569-9048(26)00126-6. [Epub ahead of print]347 104667
       INTRODUCTION: Respiratory involvement is a major determinant of prognosis in motor neurone disease (MND; or amyotrophic lateral sclerosis), yet conventional static respiratory measures provide limited information about how much available diaphragm thickening capacity is recruited during quiet breathing. We evaluated diaphragm reserve utilisation (RU), an ultrasound-derived ratio of tidal diaphragm thickening relative to maximal diaphragm thickening, as a novel physiological descriptor in MND.
    METHODS: In a prospective observational study, 38 patients with MND and 20 healthy controls underwent right hemidiaphragm ultrasound to measure thickness at end-tidal expiration, peak tidal inspiration and peak maximal inspiration. Thickening fractions and RU were calculated. Between-group differences in diaphragm ultrasound indices were assessed. Secondary analyses examined relationships between RU, respiratory function and survival.
    RESULTS: Tidal diaphragm thickening fraction was similar between patients with MND and controls, whereas maximal thickening fraction was lower in MND, resulting in higher RU in MND than controls. This pattern indicates that patients with MND maintained tidal diaphragm thickening while using a greater proportion of their available maximal thickening capacity. Higher RU was also associated with shorter survival, supporting its potential physiological and clinical relevance.
    CONCLUSION: Diaphragm reserve utilisation describes the proportion of measured diaphragm thickening capacity recruited during tidal breathing. Patients with MND demonstrated preserved tidal thickening despite reduced maximal thickening capacity, resulting in higher RU than healthy controls. This supports RU as a novel physiological index of relative diaphragm thickening reserve utilisation. The relationship between RU and survival warrants validation in larger prospective cohorts.
    Keywords:  Diaphragm reserve utilisation; Diaphragm ultrasound; Diaphragmatic dysfunction; Motor neurone disease; Neuromuscular respiratory weakness; Physiological reserve; Respiratory muscle function
    DOI:  https://doi.org/10.1016/j.resp.2026.104667
  65. Curr Issues Mol Biol. 2026 Oct 21. pii: 1087. [Epub ahead of print]48(10):
      Oxidative stress contributes to the pathophysiology of diverse neurodegenerative diseases and acute brain injuries. Pomegranate Seed Oil (PSO) is rich in punicic acid (PA), an omega-5 fatty acid with reported antioxidant and anti-inflammatory properties. However, conventional PSO and standard antioxidants show limited clinical success due to poor solubility, rapid degradation, low bioavailability, and limited delivery cross the blood-brain barrier (BBB). To address these limitations, GranaGard® (Nano-PSO), a self-emulsifying nanoformulation, was developed to improve the bioavailability and CNS delivery of PSO-derived compounds. Nano-PSO significantly increases systemic absorption and brain accumulation of its bioactive metabolite, neuroprotective conjugated linoleic acid (CLA). In a transgenic mouse model of Creutzfeldt-Jakob Disease (CJD), continuous Nano-PSO administration was reported to delayed disease onset, prolong survival, reduce lipid oxidation, preserve neuronal viability, and increase neurogenesis. Beyond CJD, Nano-PSO showed potential neuroprotective effects in various neurological diseases and brain injury models, although the magnitude and consistency of these effects varied across models. In a small preliminary clinical study in Multiple Sclerosis (MS), Nano-PSO treatment was associated with improved verbal learning in a within-group analysis, although large controlled studies are needed. By improving pharmacokinetic barriers, Nano-PSO may offer a promising, potent strategy for mitigating neurodegeneration associated with oxidative stress. These preliminary findings warrant further investigation, including independent replication and controlled clinical studies to establish the reproducibility and clinical relevance of Nano-PSO.
    Keywords:  Nano-PSO/GranaGard®; neurodegenerative diseases; neuroprotection; oxidative stress; punicic acid (PA)
    DOI:  https://doi.org/10.3390/cimb48101087
  66. Nat Med. 2026 Oct 27.
      Amyotrophic lateral sclerosis is a fatal neurodegenerative disease increasingly linked to T cell responses, although the mechanisms driving T cell activation and disease progression remain unclear. Here we used single-cell RNA and T cell receptor sequencing, longitudinal immune profiling and imaging flow cytometry to identify long-lived intrathecal clonotypes and antigen-presenting cell-T cell complexes displaying features of immunological synapse formation, consistent with intrathecal antigen presentation. Higher frequencies of CD4+ effector, CD4+ regulatory and CD8+ T cells in cerebrospinal fluid (CSF) were associated with slower disease progression, whereas increased circulating CD4+ effector and regulatory T cells were associated with faster progression. T cell clonotypes shared between blood and CSF exhibited distinct transcriptional states. Finally, frequencies of cytomegalovirus-specific T cells in CSF and anticytomegalovirus serum antibodies were correlated with faster progression and shorter survival in sporadic amyotrophic lateral sclerosis. These findings reveal compartmentalized immune dynamics, largely contrasting protective intrathecal responses with harmful systemic activation.
    DOI:  https://doi.org/10.1038/s41591-026-04728-5
  67. Neurol Int. 2026 Oct 15. pii: 193. [Epub ahead of print]18(10):
       BACKGROUND/OBJECTIVES: Neurosyphilis is a recognized treatable mimic of amyotrophic lateral sclerosis (ALS); syphilis serology is commonly included in the work-up of suspected motor neuron disease. We describe the converse situation: neurosyphilis that delayed recognition of coexisting ALS.
    METHODS: A 46-year-old man with type 2 diabetes mellitus and degenerative spine disease presented with a six-month history of progressive limb weakness and gait disturbance. Serum syphilis serology was reactive (Venereal Disease Research Laboratory [VDRL] titer 1:32; Treponema pallidum hemagglutination assay [TPHA] titer 1:20,480), and cerebrospinal fluid (CSF) showed a mild mononuclear pleocytosis with raised protein and immunoglobulin G. Neurosyphilis was diagnosed and treated with a 14-day course of intravenous penicillin. The subsequent course was followed with neuroimaging and electrodiagnostic studies.
    RESULTS: Despite treatment and resolution of the CSF pleocytosis, weakness and wasting progressed and bulbar involvement developed. Examination showed combined upper and lower motor neuron signs, electromyography showed an anterior horn cell pattern with widespread fasciculations, and cervical spine imaging showed degenerative changes without spinal cord compression. ALS was diagnosed at a later neurological admission.
    CONCLUSIONS: Identifying a treatable mimic does not close the diagnostic process. Combined upper and lower motor neuron signs that continue to progress despite adequate treatment of neurosyphilis should prompt early electrodiagnostic evaluation for ALS, even though the relative contribution of each condition may remain uncertain.
    Keywords:  ALS mimic; Treponema pallidum; amyotrophic lateral sclerosis; case report; electromyography; nerve conduction studies; neurosyphilis; syphilitic amyotrophy
    DOI:  https://doi.org/10.3390/neurolint18100193
  68. Mov Disord. 2026 Oct 28.
      The neuropathology of Parkinson's disease (PD) is characterized in part by the degeneration of catecholaminergic neurons, particularly dopaminergic neurons in the substantia nigra pars compacta (SNpc) and noradrenergic neurons in the locus coeruleus (LC), yet no validated in vivo biomarker quantifies this process. Neuromelanin-sensitive magnetic resonance imaging (NM-MRI) enables noninvasive assessment of these neuronal populations, although relationships with clinical severity, disease burden, and progression remain incompletely defined. We conducted the first Preferred Reporting Items for Systematic Reviews and Meta-Analyses (PRISMA)-guided systematic review and random-effects meta-analysis examining associations between NM-MRI measures and clinical outcomes in PD, including subgroup, meta-regression, and sensitivity analyses. Reduced NM-MRI measures were associated with greater motor impairment (18 studies; pooled r = -0.406), longer disease duration (14; r = -0.426), higher Hoehn and Yahr stage (10; r = -0.336), and higher levodopa equivalent daily dose (6; r = -0.337) (all P < 0.001). Thirty-nine studies (1983 patients with PD) were included in the systematic review. Narrative synthesis demonstrated distinct SNpc/LC associations: SNpc measures were primarily associated with motor dysfunction and disease stage, displaying hemispheric asymmetry, intranigral topography, and phenotype-specific patterns, whereas LC measures were preferentially linked to cognitive, affective, autonomic, and sleep-related symptoms. Four longitudinal studies (~1.5-3 years) reported declines in selected NM-MRI measures (~5%-19% annually). Multimodal studies suggested NM-MRI captures a complementary dimension of nigrostriatal pathology alongside dopaminergic, iron-sensitive, and diffusion-based markers. NM-MRI provides a biologically interpretable in vivo measure of catecholaminergic neuron integrity and survival in PD, with consistent cross-sectional associations with clinical disease burden. Emerging longitudinal and multimodal evidence supports its potential as a progression-sensitive imaging biomarker for disease-modifying clinical trials. © 2026 The Author(s). Movement Disorders published by Wiley Periodicals LLC on behalf of International Parkinson and Movement Disorder Society.
    Keywords:  Parkinson's disease; imaging biomarker; locus coeruleus; neuromelanin‐sensitive MRI; substantia nigra
    DOI:  https://doi.org/10.1002/mds.70588
  69. Mult Scler Relat Disord. 2026 Oct 26. pii: S2211-0348(26)01062-X. [Epub ahead of print]116 108027
       BACKGROUND: Neuromyelitis optica spectrum disorder (NMOSD) is a severe autoimmune astrocytopathy in which magnetic resonance imaging (MRI) plays a central role in diagnosis, relapse confirmation, differential diagnosis, and longitudinal monitoring. Despite its clinical relevance, standardized MRI recommendations tailored to regional practice are lacking, particularly in Latin America (LATAM), where access to imaging resources and expertise is heterogeneous.
    METHODS: Using a modified RAND/UCLA Delphi methodology, a multidisciplinary panel of LATAM experts in neurology, neuroimmunology, neuroradiology, and methodology developed consensus recommendations on the use of MRI in NMOSD. Statements were informed by a narrative review of the literature and rated using a 9-point Likert scale across iterative rounds. Consensus was predefined as a median score ≥7 with limited dispersion. Recommendations were stratified according to feasibility in real-world LATAM settings.
    RESULTS: Consensus was achieved for use of MRI at disease onset, relapse assessment, routine follow-up, differential diagnosis, evaluation of disease activity and treatment response, and the role of advanced techniques and artificial intelligence (AI). Standardized brain and spinal cord MRI are recommended at diagnosis, complemented by orbital imaging when optic neuritis is suspected. MRI contributes substantially to relapse adjudication, particularly in clinically mild or ambiguous presentations. During follow-up, MRI assists in differential diagnosis, detection of subclinical activity, prognostication, and treatment monitoring, although routine contrast use is not required in stable patients. Advanced MRI and AI-based tools are considered complementary, with current utility focused on research and registry-based applications.
    CONCLUSIONS: These LATAM-adapted consensus recommendations provide a practical, evidence-informed framework for MRI use in NMOSD, aiming to improve diagnostic accuracy, harmonize imaging practices, and optimize patient management across diverse healthcare settings.
    Keywords:  AQP4-IgG; Consensus recommendation; Latin America; MRI; NMOSD
    DOI:  https://doi.org/10.1016/j.msard.2026.108027
  70. PLoS One. 2026 ;21(10): e0360617
      Alzheimer's disease (AD), Parkinson's disease (PD), and dementia with Lewy bodies (DLB) are proteinopathies characterized by pathological accumulation of amyloid beta, phosphorylated-tau, and alpha-synuclein. Impaired clearance of these proteins is thought to contribute to disease pathogenesis, whereas preserved or enhanced clearance may be compensatory. Beyond intracellular degradation within neurons and glial cells, an extracellular clearance pathway, the glymphatic system, facilitates cerebrospinal fluid flow into perivascular spaces, exchange with interstitial fluid, and subsequent clearance from the brain. Glymphatic transport may therefore be critical for removal of excess proteins and metabolic waste, and its dysfunction could promote protein aggregation and neurodegeneration. The Glymphatic's Role In Proteinopathies (GRIP) study is an observational case-control imaging and biomarker study comparing glymphatic clearance in patients with AD, PD, and DLB versus healthy controls. We aim to recruit 70 participants: PD (n = 20), DLB (n = 10), AD (n = 20), and age- and sex-matched healthy controls (n = 20). The AD group will be stratified by pathology, with half amyloid-positive/tau-negative (A + T-) and half amyloid- and tau-positive (A + T+). The PD group will be stratified by disease duration. Participants will undergo baseline MRI followed by intrathecal injection of gadobutrol (0.25 mmol) and serial MRI at 5, 24, 48, and 72 hours. Influx and efflux of tracer will be modeled from T1 signal changes. Blood will be sampled repeatedly from 1 to 72 hours; cerebrospinal fluid will be collected at baseline. Individual glymphatic clearance will be estimated using population pharmacokinetic methods, where gadobutrol serves as a tracer. Sleep will be monitored with triaxial accelerometry and sleep diaries. The primary outcome is group differences in glymphatic clearance metrics between each disease group and controls; secondary analyses will explore associations with cognition, disease severity and duration, sleep quality, and cerebrospinal fluid protein levels.
    DOI:  https://doi.org/10.1371/journal.pone.0360617
  71. Cell Mol Neurobiol. 2026 Jul 31. pii: 157. [Epub ahead of print]46(1):
      Neurodegenerative disorders involve a strong inflammatory component, yet the underlying inflammatory mechanisms may be heterogeneous across disease stage, cell type, and systemic context. A key unresolved question is how cellular and systemic stress is converted into sustained neuroinflammation. The cyclic GMP-AMP synthase (cGAS)-stimulator of interferon genes (STING) pathway is an innate DNA-sensing hub that translates mislocalized self-DNA - derived from mitochondrial stress and mtDNA leakage, nuclear envelope instability, micronuclei formation, or impaired nucleic-acid disposal - into type I interferon, NF-kB, autophagy-related, and senescence-associated inflammatory programs. Rather than treating cGAS-STING as a universal disease-defining pathway, this review frames it as a context-dependent amplifier that becomes pathogenic when DNA-DAMP burden, defective mitochondrial quality control, neurovascular "leakage", and glial priming converge. We synthesize cell-type-specific evidence in microglia, astrocytes, neurons, and the neurovascular unit; compare mechanistic involvement across Alzheimer's disease, Parkinson's disease dementia and Lewy body disease, amyotrophic lateral sclerosis/frontotemporal dementia (ALS/FTD), vascular and acute brain injury, and systemic inflammatory encephalopathies; and organize periphery-to-brain communication axes using an explicit evidence-grading framework. A distinctive contribution of this review is a two-hit model in which systemic inflammatory stressors and barrier dysfunction first lower cognitive resilience, followed by brain-resident mitochondrial/DNA damage programs that lock in complement-linked synaptopathy. We also evaluate pharmacological and lifestyle-based modulation, emphasizing biomarker-enriched trial design, CNS exposure, compartment-specific target engagement, and immune-safety constraints. This framework aims to clarify when, where, and in whom cGAS-STING modulation may preserve synapses and cognition without unacceptable immune trade-offs.
    Keywords:  CGAS-STING; Cognitive dysfunction; Neuroinflammation; Peripheral-brain axis
    DOI:  https://doi.org/10.1007/s10571-026-01786-8
  72. Int J Mol Sci. 2026 Oct 13. pii: 9080. [Epub ahead of print]27(20):
      Dihydromyricetin (DHM) is a bioactive polyphenol with broad therapeutic potential, including strong anti-inflammatory activity. Importantly, DHM has been shown to cross the blood-brain barrier (BBB), enabling pharmacological activity within the central nervous system (CNS) and positioning it as a candidate for CNS disorders in which neuroinflammation plays a central role, including Alzheimer's disease, Parkinson's disease, and stroke. Therapeutics such as DHM, which address neuroinflammation, are of increasing interest. Across CNS disease models, DHM's effects show recurring convergence on NF-κB suppression, NLRP3 inflammasome inhibition, and autophagy regulation, alongside context-specific mechanisms involving oxidative stress, ferroptosis, neurotrophic signaling, and peripheral gut-CNS communication. This review examines the evidence for DHM as a neuroinflammatory modulator, focusing on the mechanisms by which it exerts its therapeutic effects. By doing so, we aim to support its translational potential as a natural product for improving human health.
    Keywords:  NF-κB; NLRP3 inflammasome; autophagy; central nervous system; dihydromyricetin; neurodegenerative diseases; neuroinflammation; oxidative stress; stroke
    DOI:  https://doi.org/10.3390/ijms27209080
  73. Biomedicines. 2026 Oct 05. pii: 2251. [Epub ahead of print]14(10):
      Background/Objectives: The blood-brain barrier (BBB) severely limits the intratumoral delivery of systemically administered therapeutics in diffuse gliomas, including glioblastoma (GBM), contributing to the persistently poor prognosis of these tumors. Focused ultrasound (FUS) combined with microbubble agents enables transient, spatially targeted, and reversible BBB opening (BBBO), offering a non-invasive strategy to enhance drug delivery in this setting. Despite a rapidly growing body of clinical evidence, a systematic synthesis of outcomes across FUS platforms, drug regimens, and study designs is currently lacking. This systematic review aims to critically appraise the available clinical evidence on FUS-mediated BBBO for enhanced drug delivery in adult patients with diffuse gliomas. Methods: A systematic search of PubMed/MEDLINE and Scopus was performed using pre-specified search terms (last search: June 2026). Eligible studies included clinical trials and cohort studies enrolling adult patients (≥18 years) with histologically confirmed diffuse glioma (WHO grades II-IV) who underwent FUS-BBBO for therapeutic drug delivery enhancement. Two reviewers independently screened records and extracted data using a standardized form. Study quality was assessed using the NIH Quality Assessment Tool for Before-After Studies (single-arm studies) and the ROBINS-I tool (comparative studies). The review was retrospectively registered on OSF. Results were synthesized narratively due to study heterogeneity. Results: Eight publications from seven independent clinical studies were included. Across these publications, 68 patient entries were reported; however, because of overlapping populations across publications, the number of unique patients could not be precisely determined. Two FUS platforms were employed, with the ExAblate Neuro system (220-230 kHz) used in six out of seven cohorts. BBB opening was confirmed in all studies, with target sonication success rates of 92.4-100%. No procedure-related serious adverse events attributable to FUS-BBBO were reported across any study. Transient T2/SWAN hypointense foci were observed in a subset of patients, consistently asymptomatic and histologically benign. Direct intratumoral drug quantification was feasible in two pre-surgical studies, demonstrating a 2.2-fold increase in drug accumulation in FUS-treated versus untreated tissue (p < 0.01). The only comparative study reported a statistically significant improvement in overall survival (median 31.3 vs. 19.3 months; HR 0.50, p = 0.009) and progression-free survival (median 13.5 vs. 8.1 months; HR 0.55, p = 0.020) versus the controls. Conclusions: FUS-mediated BBBO is a safe and feasible approach for enhancing drug delivery in adult diffuse glioma patients across multiple platforms and drug combinations. Preliminary comparative data suggest a potential survival benefit in newly diagnosed GBM; however, these findings are based on a single non-randomized study and require confirmation in prospective randomized controlled trials.
    Keywords:  MRgFUS; blood–brain barrier opening; drug delivery; focused ultrasound; glioblastoma; glioma; microbubbles; neuro-oncology; systematic review
    DOI:  https://doi.org/10.3390/biomedicines14102251
  74. Pharmacol Res. 2026 Oct 29. pii: S1043-6618(26)01629-4. [Epub ahead of print] 109714
      Neurodegenerative disorders are a leading cause of disability and mortality globally, but effective disease-modifying therapeutic strategies are still largely unavailable. Scutellarin is a flavonoid glycoside extracted from Erigeron breviscapus (Vant.) Hand-Mazz. It has been widely studied in preclinical models of neurodegenerative disorders. In this study, we performed a systematic review of preclinical animal studies. We combined comprehensive database retrieval with quantitative synthesis of eligible outcomes. The pooled results demonstrated that scutellarin significantly reduced cerebral infarct volume and improved neurological deficit scores in cerebral ischemia-reperfusion models. It also ameliorated learning and memory impairments in experimental Alzheimer's disease (AD) models. Consistent neuroprotective effects were also found in models of depression, anxiety, Parkinson's disease, etc. Mechanistic analysis indicated that scutellarin produces multi-level neuroprotective effects. It acts by reducing oxidative stress, inhibiting neuroinflammation, suppressing apoptosis, stabilizing the neurovascular unit and other neurobiological processes. This review first evaluated the preclinical efficacy of scutellarin through systematic review and meta-analysis. It then integrated cross-disease mechanisms with network pharmacology, reverse virtual screening and molecular docking to identify computationally predicted targets. Although scutellarin shows promising preclinical effects, its clinical translation faces major limitations. These limitations include low oral bioavailability, poor blood-brain barrier (BBB) penetration and insufficient data on brain exposure. Overall, scutellarin is a multi-target neuroprotective candidate. Future studies should focus on target validation, exposure-response modeling, delivery optimization and clinically relevant translational evaluation.
    Keywords:  Scutellarin; apoptosis; neurodegenerative disorders; oxidative stress; pharmacology
    DOI:  https://doi.org/10.1016/j.phrs.2026.109714
  75. Mult Scler. 2026 Oct 27. 13524585261490852
      Costimulatory signaling is essential for T-cell activation, tolerance, and immune homeostasis. Dysregulation of these pathways contributes to autoimmune diseases, including multiple sclerosis. Therapeutic targeting of costimulatory molecules, particularly the CD40-CD40L axis, has demonstrated clinical success in several autoimmune conditions, including multiple sclerosis. This review integrates mechanistic insights from experimental models with clinical data to examine the effects of CD40L blockade across diverse immune and central nervous system-resident cell populations. Preclinical models highlight the complex interplay between immune cells and central nervous system-resident cells beyond costimulatory signaling alone. Clinical mechanistic studies support CD40L blockade as a promising therapeutic strategy for multiple sclerosis.
    Keywords:  biomarkers; clinical trial; disease-modifying therapies; glia; immunology; multiple sclerosis
    DOI:  https://doi.org/10.1177/13524585261490852
  76. Diagnostics (Basel). 2026 Oct 10. pii: 3288. [Epub ahead of print]16(20):
      Background/Objectives: A common diagnosis for lumbar disc herniation is an image taken with Magnetic Resonance Imaging (MRI). Due to the need for expertise during manual interpretation of MRI scans by specialists, the process is very time consuming. The use of a machine learning (ML)-based pathway to classify lumbar MRI images as either "normal" or "herniated" represents an efficient way to analyse MRI scans seeking similar pathologies. Methods: The proposed methodology transforms original lumbar MRIs (from colour to greyscale), resizes them, filters, and normalises them (using bilateral algorithms) before conducting extraction of features using PCA-based decomposition. A total of ten classical ML classifiers were evaluated using five-fold outer and three-fold inner nested cross-validation, with the number of PCA components selected exclusively within the inner folds. Results: Extra Trees achieved the highest F1-score of 85.86% (95% CI: 84.16-87.44%) and the highest ROC-AUC of 90.96% (95% CI: 89.27-92.54%), with an accuracy of 84.29%, precision of 82.03%, recall of 90.07%, and specificity of 77.79%. Random Forest achieved the highest accuracy of 84.36% (95% CI: 82.40-86.26%), although its overall performance was comparable to that of Extra Trees. Conclusions: The findings support the potential of traditional machine learning classifiers for binary classification within the evaluated image-level dataset, while maintaining a relatively simple design and computational efficiency. No direct empirical comparison with deep learning models was conducted in this study.
    Keywords:  extra trees; feature standardization; image preprocessing; intensity normalization; lumbar disc herniation; machine learning; magnetic resonance imaging (MRI); nested cross-validation; principal component analysis (PCA); random forest; smoothing
    DOI:  https://doi.org/10.3390/diagnostics16203288
  77. J Transl Med. 2026 Oct 21. pii: 1376. [Epub ahead of print]24(1):
       BACKGROUND: High-altitude exposure has been linked to an increased risk of Parkinson's disease (PD), potentially through hypoxic neuronal damage, yet the involvement of α-synuclein (α-syn) remains poorly understood. This study integrates population-based surveys, animal experiments, and clinical cross-sectional data to elucidate the role of high-altitude environments in PD pathogenesis.
    METHODS: A cross-sectional study was conducted among middle-aged and elderly high-altitude residents. Additional cohorts (low-altitude PD patients, low-altitude controls, and high-altitude controls) were enrolled for plasma and erythrocytic α-syn measurement, and a subset of PD patients underwent transcranial sonography to assess correlations between erythrocyte indices and substantia nigra echogenicity. A53T transgenic mice were exposed to high altitude for six months and evaluated by behavioral tests, omics sequencing, α-syn assays, and immunohistochemistry. Erythrocyte-derived extracellular vesicles from PD patients were intravenously injected into wild-type mice to assess brain entry.
    RESULTS: The crude prevalence of PD tended to be higher in high-altitude populations than the national average. A53T mice exposed to high altitude displayed more severe motor deficits, elevated brain α-syn levels, and pronounced dopaminergic neuron loss. Omics analyses revealed enrichment of pathways related to IL-17, sphingosine-1-phosphate signaling, and oxidative stress in brain tissue from high-altitude versus low-altitude A53T mice, suggesting blood-brain barrier disruption and impaired α-syn clearance. In peripheral blood, both high-altitude mice and humans exhibited elevated α-syn levels compared with their low-altitude counterparts, and erythrocyte indices correlated positively with α-syn levels. After normalization to erythrocyte count and hemoglobin, however, erythrocytic α-syn did not differ between high-altitude and low-altitude controls. In mice, intravenously injected human-derived erythrocytic vesicles entered the brain.
    CONCLUSIONS: Chronic high‑altitude exposure is associated with peripheral and central α‑syn accumulation, which may be driven by a hypoxia‑induced erythrocyte pool expansion and increased α-syn burden, potentially aggravating PD‑related neuropathology.
    Keywords:  Alpha-synuclein; Erythrocyte; High altitude; Hypoxia; Parkinson’s disease
    DOI:  https://doi.org/10.1186/s12967-026-09103-z
  78. Neuroepidemiology. 2026 Oct 28. 1
       BACKGROUND: Neurodegenerative diseases (NDDs), including Alzheimer's disease and other dementias (ADOD), Parkinson's disease (PD), and motor neuron disease (MND), represent a mounting public health challenge in China amid rapid population aging. A systematic deconstruction of their epidemiological transition using the most recent data remains lacking.
    METHODS: Data from the Global Burden of Disease Study 2023 were utilized to examine temporal trends (1990-2023) for ADOD, PD, and MND in China. Age-standardized rates of incidence (ASIR), prevalence (ASPR), mortality (ASMR), and disability-adjusted life-years (ASDR) were analyzed. Joinpoint regression was used to identify significant inflection points. Decomposition analysis quantified the contributions of population aging, population growth, and epidemiological change. And bayesian age-period-cohort models projected trends to 2035.
    RESULTS: From 1990 to 2023, the ASIR for ADOD (EAPC 0.41; 95% CI 0.33 to 0.49) and PD (EAPC 0.84; 95% CI 0.76 to 0.92) rose significantly. Between 2019 and 2023, multiple indicators across the three diseases demonstrated a consistently synchronous upward trend. This acceleration coincided with the COVID-19 pandemic. Decomposition demonstrated that population aging was the dominant driver. Sex-specific disparities were pronounced. Females bore a higher ADOD burden, whereas males predominated in PD. ASIR and ASPR are expected to rise, while ASMR and ASDR are projected to decline for ADOD and PD. For MND, only the ASPR indicated a brief, peaked rise in the predicted trends.
    CONCLUSIONS: In the field of neurodegenerative diseases, China is projected to undergo an epidemiological transition characterized by chronicization. This trend calls for systematic adjustments in healthcare services, long-term care systems, and social support structures. Sex and gender differences further underscore the need for gender-sensitive prevention, clinical management, and care strategies to prevent the further widening of inequalities. Population aging remains a critical factor that cannot be overlooked. Therefore, there is an urgent need to establish a proactive, gender-sensitive framework for system-wide restructuring that incorporates long-term monitoring and oversight.
    DOI:  https://doi.org/10.1159/ned/adwag059
  79. J Am Chem Soc. 2026 Sep 30. 148(38): 41137-41150
      Targeted protein degradation has emerged as a transformative therapeutic strategy, yet its application to neurodegenerative diseases remains fundamentally constrained by the blood-brain barrier (BBB) and lesion specificity. Critically, the BBB undergoes age-dependent functional remodeling, further exacerbating the difficulty of therapeutic intervention. Here we report BBB-permeable macrocyclic chimeras (BmTACs), a modular degradation platform for selective elimination of activated death-associated protein kinase 1 (DAPK1) in the aging brain. BmTACs harness a macrocyclic peptide shuttle that exploits age-upregulated caveolae-mediated transcytosis in brain endothelial cells to achieve efficient BBB traversal and neuron-targeting. A reactive oxygen species (ROS)-responsive caging group on the von Hippel-Lindau ligand enables conditional PROTAC activation exclusively within the high-ROS microenvironment of Alzheimer's disease lesions, minimizing off-target degradation. Systemic administration of BmTACs in aged APP/PS1 mice achieved potent degradation of activated DAPK1, attenuated amyloid-β deposition and Tau hyperphosphorylation, and improved cognition. This work establishes a modular, senescence-adapted paradigm for targeted protein degradation in the aging central nervous system.
    DOI:  https://doi.org/10.1021/jacs.6c11943
  80. J Inflamm Res. 2026 ;19 635719
       Purpose: Research on B cells in central nervous system (CNS) diseases rests on a mature multiple sclerosis (MS) literature, whereas evidence in CNS injury and neurodegeneration is still emerging. We mapped publications from 2006 to 2026 and separated bibliometric visibility from mechanistic maturity.
    Methods: We searched the Web of Science Core Collection (WoSCC) on August 17, 2026, for English-language records carrying the Article document-type tag and published from January 1, 2006, through August 17, 2026. Two reviewers independently screened all records, with unresolved disagreements adjudicated by a third reviewer. Publication trends, collaboration, co-citation, journal flows, citation bursts, and keyword evolution were analyzed using VOSviewer, CiteSpace, bibliometrix, R, and SCImago Graphica. Search materials, parameters, and source tables were archived.
    Results: After database-level limits, 2,701 records were screened; 467 (17.3%) were excluded and 2,234 (82.7%) included. The corpus had accrued 91,218 WoSCC citations. Annual output rose from 91 articles in 2016 to 231 in 2025; 173 articles from 2026 represent a partial year. The United States contributed the most articles, and the University of California, San Francisco ranked first after affiliation normalization. Co-citation and keyword analyses showed an MS/experimental autoimmune encephalomyelitis (EAE)-centered foundation built around B-cell depletion trials, meningeal pathology, diagnostic criteria, and regulatory B-cell biology. Recent bursts included anti-CD20 therapy, single-cell RNA sequencing, autoimmune encephalitis, ischemic stroke, Mendelian randomization, B-cell depletion, and Alzheimer disease.
    Conclusion: B-cell-related CNS research has expanded, but evidence maturity remains disease-specific. MS/EAE provides the clearest foundation. Findings in CNS injury, neurodegeneration, and candidate peripheral-CNS routes remain context-dependent and require validation by disease, anatomical compartment, B-cell state, and stage. Bibliometric prominence reveals attention, not shared causality or therapeutic efficacy.
    Keywords:  B cells; bibliometric analysis; central nervous system; multiple sclerosis; neuroinflammation; science mapping
    DOI:  https://doi.org/10.2147/JIR.S635719
  81. Biomed Pharmacother. 2026 Oct 27. pii: S0753-3322(26)01024-3. [Epub ahead of print]204 119988
      Our investigation aimed to delineate the pharmacokinetic parameters of the most commonly used TRPA1 receptor antagonists, A967079 and HC-030031, concerning their drug-likeness and penetration into the central nervous system (CNS). Both substances were tested at two different dosages and two different formulations using the intraperitoneal and subcutaneous routes of administration. We determined the drug-like properties of the substances using several different models. Our findings demonstrate that both substances are able to pass the blood-brain barrier and remain in the CNS for a relatively long period when administered via the appropriate mode and formulation. In the case of A967079, effective concentrations can not only be achieved but also maintained for hours in both plasma and brain tissue. In the case of HC-030031, a shorter residence time and less favourable kinetics are observed. During the study, elimination half-lives were determined separately for plasma and brain tissue, and the brain-to-plasma distribution ratio was calculated. In addition to elimination kinetics, the temporal distribution of the compounds in the liver and kidney was also assessed. Overall, these results provide important pharmacokinetic insights that may facilitate further investigation of TRPA1 ion channel inhibition as a potential therapeutic strategy.
    Keywords:  In silico pharmacology; In vivo pharmacology; Pharmacokinetics; Receptor antagonist; TRPA1; TRPA1 antagonist
    DOI:  https://doi.org/10.1016/j.biopha.2026.119988
  82. Int J Mol Sci. 2026 Oct 10. pii: 8990. [Epub ahead of print]27(20):
      Neurological disorders represent a leading cause of global disability and mortality. Given that current single-target therapies often fail to halt disease progression or cross the blood-brain barrier (BBB), novel therapeutic strategies are urgently needed. Endogenous lipid networks offer promising targets. They are major structural components of the central nervous system (CNS) that provide multi-target neuroprotection essential for homeostasis and can bypass BBB restrictions naturally or via brain-penetrant small-molecule modulation. Among these lipids, arachidonic acid (AA) accounts for approximately 20% of total neuronal fatty acids. Upon cellular activation, while the cyclooxygenases (COXs) and lipoxygenases (LOXs) pathways yield pro-inflammatory mediators targeted by classic drugs, the cytochrome P450 (CYP450) cascade generates protective epoxyeicosatrienoic acids (EETs), which serve as fundamental regulators of systemic and neural homeostasis. Within the CNS, EETs act as crucial protectors of the neurovascular unit (NVU) by regulating cerebral blood flow (CBF), maintaining BBB integrity, and promoting angiogenesis. Furthermore, they actively mitigate neuroinflammation by suppressing microglial activation, reducing oxidative stress, and inhibiting neuronal apoptosis. Through these multifaceted mechanisms, alongside the enhancement of neurogenesis and synaptic plasticity, EETs effectively protect the brain against ischemic stroke, neurodegenerative diseases, and other neurological insults. Consequently, this article comprehensively reviews the physiological roles, underlying mechanisms, and regulatory factors of EETs in the nervous system. Ultimately, by highlighting the translational potential of targeted soluble epoxide hydrolase (sEH) inhibition and EET elevation, this review aims to pave the way for innovative neuroprotective therapies.
    Keywords:  cytochrome P450 monooxygenase; epoxyeicosatrienoic acids; neuropsychiatric disorders; soluble epoxide hydrolase
    DOI:  https://doi.org/10.3390/ijms27208990